Readthrough-induced misincorporated amino acid ratios guide mutant-specific therapeutic approaches for two CFTR nonsense mutations
通读诱导的错误氨基酸比例可指导针对两种 CFTR 无义突变的突变体特异性治疗方法
期刊:Frontiers in Pharmacology
影响因子:4.4
doi:10.3389/fphar.2024.1389586
Aiswarya Premchandar, Ruiji Ming, Abed Baiad, Dillon F Da Fonte, Haijin Xu, Denis Faubert, Guido Veit, Gergely L Lukacs