Potent and uniform fetal hemoglobin induction via base editing
通过碱基编辑实现强效、均匀的胎儿血红蛋白诱导
期刊:Nature Genetics
影响因子:31.7
doi:10.1038/s41588-023-01434-7
Thiyagaraj Mayuranathan #, Gregory A Newby #, Ruopeng Feng, Yu Yao, Kalin D Mayberry, Cicera R Lazzarotto, Yichao Li, Rachel M Levine, Nikitha Nimmagadda, Erin Dempsey, Guolian Kang, Shaina N Porter, Phillip A Doerfler, Jingjing Zhang, Yoonjeong Jang, Jingjing Chen, Henry W Bell, Merlin Crossley, Se