日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction

利用单同源臂供体介导的内含子靶向基因整合进行精确的体内基因组编辑,以纠正遗传疾病。

Keiichiro Suzuki,Mako Yamamoto,Reyna Hernandez-Benitez,Zhe Li,Christopher Wei,Rupa Devi Soligalla,Emi Aizawa,Fumiyuki Hatanaka,Masakazu Kurita,Pradeep Reddy,Alejandro Ocampo,Tomoaki Hishida,Masahiro Sakurai,Amy N Nemeth,Estrella Nuñez Delicado,Josep M Campistol,Pierre Magistretti,Pedro Guillen,Concepcion Rodriguez Esteban,Jianhui Gong,Yilin Yuan,Ying Gu,Guang-Hui Liu,Carlos López-Otín,Jun Wu,Kun Zhang,Juan Carlos Izpisua Belmonte

In vivo genome editing via CRISPR/Cas9 mediated homology-independent targeted integration

通过 CRISPR/Cas9 介导的同源性非依赖性靶向整合进行体内基因组编辑

Keiichiro Suzuki, Yuji Tsunekawa, Reyna Hernandez-Benitez, Jun Wu, Jie Zhu, Euiseok J Kim, Fumiyuki Hatanaka, Mako Yamamoto, Toshikazu Araoka, Zhe Li, Masakazu Kurita, Tomoaki Hishida, Mo Li, Emi Aizawa, Shicheng Guo, Song Chen, April Goebl, Rupa Devi Soligalla, Jing Qu, Tingshuai Jiang, Xin Fu, Mar

Modelling Fanconi anemia pathogenesis and therapeutics using integration-free patient-derived iPSCs

利用无整合患者来源的iPSCs模拟范可尼贫血的发病机制和治疗方法

Guang-Hui Liu # ,Keiichiro Suzuki #,Mo Li #,Jing Qu # ,Nuria Montserrat,Carolina Tarantino,Ying Gu,Fei Yi,Xiuling Xu,Weiqi Zhang,Sergio Ruiz,Nongluk Plongthongkum,Kun Zhang,Shigeo Masuda,Emmanuel Nivet,Yuji Tsunekawa,Rupa Devi Soligalla,April Goebl,Emi Aizawa,Na Young Kim,Jessica Kim,Ilir Dubova,Ying Li,Ruotong Ren,Chris Benner,Antonio Del Sol,Juan Bueren ,Juan Pablo Trujillo,Jordi Surralles,Enrico Cappelli,Carlo Dufour,Concepcion Rodriguez Esteban,Juan Carlos Izpisua Belmonte