Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction
利用单同源臂供体介导的内含子靶向基因整合进行精确的体内基因组编辑,以纠正遗传疾病。
期刊:Cellular Signalling
影响因子:28.1
doi:10.1038/s41422-019-0213-0
Keiichiro Suzuki,Mako Yamamoto,Reyna Hernandez-Benitez,Zhe Li,Christopher Wei,Rupa Devi Soligalla,Emi Aizawa,Fumiyuki Hatanaka,Masakazu Kurita,Pradeep Reddy,Alejandro Ocampo,Tomoaki Hishida,Masahiro Sakurai,Amy N Nemeth,Estrella Nuñez Delicado,Josep M Campistol,Pierre Magistretti,Pedro Guillen,Concepcion Rodriguez Esteban,Jianhui Gong,Yilin Yuan,Ying Gu,Guang-Hui Liu,Carlos López-Otín,Jun Wu,Kun Zhang,Juan Carlos Izpisua Belmonte