Comparative efficacy of leniolisib (CDZ173) versus standard of care on rates of respiratory tract infection and serum immunoglobulin M (IgM) levels among individuals with activated phosphoinositide 3-kinase delta (PI3Kδ) syndrome (APDS): an externally controlled study
一项外部对照研究比较了 leniolisib (CDZ173) 与标准疗法对活化磷脂酰肌醇 3-激酶 δ (PI3Kδ) 综合征 (APDS) 患者呼吸道感染率和血清免疫球蛋白 M (IgM) 水平的影响:一项外部对照研究
期刊:Clinical and Experimental Immunology
影响因子:3.8
doi:10.1093/cei/uxae107
Whalen, John; Chandra, Anita; Kracker, Sven; Ehl, Stephan; Seidel, Markus G; Gulas, Ioana; Dron, Louis; Velummailum, Russanthy; Nagamuthu, Chenthila; Liu, Sichen; Tutein Nolthenius, Joanne; Maccari, Maria Elena