Preclinical Evaluation of Foamy Virus Vector-Mediated Gene Addition in Human Hematopoietic Stem/Progenitor Cells for Correction of Leukocyte Adhesion Deficiency Type 1
泡沫病毒载体介导的基因添加在人造血干/祖细胞中治疗白细胞黏附缺陷1型的临床前评价
期刊:Human Gene Therapy
影响因子:4
doi:10.1089/hum.2022.065
Smith, Richard H; Bloomer, Hanan; Fink, Danielle; Keyvanfar, Keyvan; Nasimuzzaman, Md; Sancheznieto, Fátima; Dutta, Roop; Guenther Bui, Kacey; Alvarado, Luigi J; Bauer, Thomas R Jr; Hickstein, Dennis D; Russell, David W; Malik, Punam; van der Loo, Johannes C M; Highfill, Steven L; Kuhns, Douglas B; Pirooznia, Mehdi; Larochelle, Andre