A Phase 1, Double-Blind, Placebo-Controlled Trial of Sevasemten (EDG-5506), a Selective Modulator of Fast Skeletal Muscle Contraction, in Healthy Volunteers and Adults With Becker Muscular Dystrophy
一项针对健康志愿者和贝克尔肌营养不良症成年患者的 Sevasemten (EDG-5506)(一种选择性快速骨骼肌收缩调节剂)的 1 期双盲安慰剂对照试验
期刊:Muscle & Nerve
影响因子:3.1
doi:10.1002/mus.28444
Donovan, Joanne; Silverman, Jeffrey A; Barthel, Ben; DuVall, Michael; Madden, Molly; MacDougall, James; Kilburn, Nicole Rempel; Bronson, Abby; Evanchik, Marc; Gordon, Gilad; Koch, Kevin; Russell, Alan J