日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial

鞘内注射onasemnogene abeparvovec治疗初治脊髓性肌萎缩症患者:一项3期随机对照试验

Proud, Crystal M; Vũ, Dũng Chí; Wilmshurst, Jo M; Sanmaneechai, Oranee; Gulati, Sheffali; Xiong, Hui; Moreno, Hugo C; Tay, Stacey Kiat Hong; Thong, Meow-Keong; Born, Alfred Peter; Banzzatto Ortega, Adriana; Jong, Yuh-Jyh; Al-Muhaizea, Mohammad A; Lee, Anna W; Visootsak, Jeannie; Tauscher-Wisniewski, Sitra; Alecu, Iulian; Parlikar, Rutvick; Finkel, Richard S

Icenticaftor, a CFTR Potentiator, in COPD: A Multicenter, Parallel-Group, Double-Blind Clinical Trial

Icenticaftor(一种CFTR增强剂)治疗COPD:一项多中心、平行组、双盲临床试验

Martinez, Fernando J; Criner, Gerard J; Gessner, Christian; Jandl, Margret; Scherbovsky, Fernando; Shinkai, Masaharu; Siler, Thomas M; Vogelmeier, Claus F; Voves, Robert; Wedzicha, Jadwiga A; Bartels, Christian; Bottoli, Ivan; Byiers, Stuart; Cardenas, Pamela; Eckert, Joerg H; Gutzwiller, Florian S; Knorr, Barbara; Kothari, Mahavir; Parlikar, Rutvick; Tanase, Ana-Maria; Franssen, Frits M E