日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cyclic Peptides to Improve Delivery and Exon Skipping of Antisense Oligonucleotides in a Mouse Model for Duchenne Muscular Dystrophy

环状肽可改善杜氏肌营养不良症小鼠模型中反义寡核苷酸的递送和外显子跳跃

Silvana M G Jirka, Peter A C 't Hoen, Valeriano Diaz Parillas, Christa L Tanganyika-de Winter, Ruurd C Verheul, Begona Aguilera, Peter C de Visser, Annemieke M Aartsma-Rus

A multicenter comparison of quantification methods for antisense oligonucleotide-induced DMD exon 51 skipping in Duchenne muscular dystrophy cell cultures

一项针对杜氏肌营养不良症细胞培养物中反义寡核苷酸诱导的DMD外显子51跳跃定量方法的多中心比较研究

Monika Hiller ,Maria Sofia Falzarano ,Iker Garcia-Jimenez ,Valentina Sardone ,Ruurd C Verheul ,Linda Popplewell ,Karen Anthony ,Estibaliz Ruiz-Del-Yerro ,Hana Osman ,Jelle J Goeman ,Kamel Mamchaoui ,George Dickson ,Alessandra Ferlini ,Francesco Muntoni ,Annemieke Aartsma-Rus ,Virginia Arechavala-Gomeza ,Nicole A Datson ,Pietro Spitali

Competition for FcRn-mediated transport gives rise to short half-life of human IgG3 and offers therapeutic potential

FcRn 介导的运输竞争导致人类 IgG3 半衰期缩短,并具有治疗潜力

Nigel M Stapleton, Jan Terje Andersen, Annette M Stemerding, Stefania P Bjarnarson, Ruurd C Verheul, Jacoline Gerritsen, Yixian Zhao, Marion Kleijer, Inger Sandlie, Masja de Haas, Ingileif Jonsdottir, C Ellen van der Schoot, Gestur Vidarsson