A multicenter comparison of quantification methods for antisense oligonucleotide-induced DMD exon 51 skipping in Duchenne muscular dystrophy cell cultures
一项针对杜氏肌营养不良症细胞培养物中反义寡核苷酸诱导的DMD外显子51跳跃定量方法的多中心比较研究
期刊:PLoS One
影响因子:2.9
doi:10.1371/journal.pone.0204485
Monika Hiller ,Maria Sofia Falzarano ,Iker Garcia-Jimenez ,Valentina Sardone ,Ruurd C Verheul ,Linda Popplewell ,Karen Anthony ,Estibaliz Ruiz-Del-Yerro ,Hana Osman ,Jelle J Goeman ,Kamel Mamchaoui ,George Dickson ,Alessandra Ferlini ,Francesco Muntoni ,Annemieke Aartsma-Rus ,Virginia Arechavala-Gomeza ,Nicole A Datson ,Pietro Spitali