Validation of Duchenne muscular dystrophy candidate modifiers using a CRISPR-Cas9-based approach in zebrafish
利用基于 CRISPR-Cas9 的方法在斑马鱼中验证杜氏肌营养不良症候选修饰基因
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doi:10.1101/2025.05.20.655139
Lerma, Geremy; Ryhlick, Kamorah R; Carraher, Olivia M; Beljan, Joseph C; Amacher, Sharon L