The KHENERGY Study: Safety and Efficacy of KH176 in Mitochondrial m.3243A>G Spectrum Disorders
KHENERGY 研究:KH176 对线粒体 m.3243A>G 谱疾病的安全性和有效性
期刊:Clinical Pharmacology & Therapeutics
影响因子:6.3
doi:10.1002/cpt.1197
Mirian C H Janssen, Saskia Koene, Paul de Laat, Pleun Hemelaar, Peter Pickkers, Edwin Spaans, Rypko Beukema, Julien Beyrath, Jan Groothuis, Chris Verhaak, Jan Smeitink