Successful Therapy over 12 Months of People with Cystic Fibrosis with Rare Non-phe508del Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Mutations with Elexacaftor/Tezacaftor/Ivacaftor (ETI)

使用 Elexacaftor/Tezacaftor/Ivacaftor (ETI) 治疗 12 个月，成功治愈了患有罕见非 Phe508del 囊性纤维化跨膜传导调节因子 (CFTR) 突变的囊性纤维化患者。