Controlled access to lumasiran in primary hyperoxaluria type 1: evaluation of a new access route for orphan drugs in the Netherlands
在荷兰,对一种新的孤儿药获取途径进行评估,以控制原发性高草酸尿症1型患者获得鲁马西兰的途径。
期刊:Nephrology Dialysis Transplantation
影响因子:5.6
doi:10.1093/ndt/gfaf060
Deesker, Lisa J; Franssen, Casper F M; Dorresteijn, Eiske; van de Kar, Nicole C A J; Nurmohamed, S Azam; Severs, David; Garrelfs, Sander F; Pisters-van Roy, Anke A M G; Hollak, Carla E M; Groothoff, Jaap W