CRISPR/Cas9 DNA cleavage at SNP-derived PAM enables both in vitro and in vivo KRT12 mutation-specific targeting
CRISPR/Cas9 在 SNP 衍生的 PAM 处进行 DNA 切割,可实现体外和体内 KRT12 突变特异性靶向
期刊:Gene Therapy
影响因子:4.6
doi:10.1038/gt.2015.82
D G Courtney, J E Moore, S D Atkinson, E Maurizi, E H A Allen, D M L Pedrioli, W H I McLean, M A Nesbit, C B T Moore