Increased dystrophin production with golodirsen in patients with Duchenne muscular dystrophy
戈洛定可增加杜氏肌营养不良症患者肌营养不良蛋白的产生
期刊:Neurology
影响因子:7.7
doi:10.1212/WNL.0000000000009233
Diane E Frank, Frederick J Schnell, Cody Akana, Saleh H El-Husayni, Cody A Desjardins, Jennifer Morgan, Jay S Charleston, Valentina Sardone, Joana Domingos, George Dickson, Volker Straub, Michela Guglieri, Eugenio Mercuri, Laurent Servais, Francesco Muntoni; SKIP-NMD Study Group