Lentiviral Gene Therapy with CD34+ Hematopoietic Cells for Hemophilia A
利用CD34+造血细胞进行慢病毒基因治疗A型血友病
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa2410597
Srivastava, Alok; Abraham, Aby; Aboobacker, Fouzia; Singh, Gurbind; Geevar, Tulasi; Kulkarni, Uday; Selvarajan, Sushil; Korula, Anu; Dave, Rutvi Gautam; Shankar, Mohana; Singh, Abraham S; Jeba, Anbu; Kumaar, Navien; Benjamin, Christopher; Lakshmi, Kavitha M; Srivastava, Vivi Miriam; Shaji, Ramachandran V; Nair, Sukesh C; Brown, Harrison C; Denning, Gabriela; Lollar, Pete; Doering, Christopher B; Spencer, Trent