miR-107 represses DMPK and is sequestered by CUG repeats triggering the MSI2/miR-7 pathogenesis axis in myotonic dystrophy.
miR-107 抑制 DMPK,并被 CUG 重复序列隔离,从而触发强直性肌营养不良症中的 MSI2/miR-7 发病机制轴
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.1
doi:10.1016/j.omtn.2025.102584
Moreno N, Sabater-Arcis M, Espinosa-Espinosa J, Mulet-Rivero L, GarcÃa-España E, González-GarcÃa J, Seoane-Miraz D, Wood M J A, Varela M A, Ohana J, Sevilla T, Perez Alonso M, Bargiela A, Artero R