Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency
基因修饰干细胞治疗腺苷脱氨酶缺乏型免疫缺陷症的临床疗效
期刊:Journal of Clinical Investigation
影响因子:13.3
doi:10.1172/JCI90367
Kit L Shaw, Elizabeth Garabedian, Suparna Mishra, Provaboti Barman, Alejandra Davila, Denise Carbonaro, Sally Shupien, Christopher Silvin, Sabine Geiger, Barbara Nowicki, E Monika Smogorzewska, Berkley Brown, Xiaoyan Wang, Satiro de Oliveira, Yeong Choi, Alan Ikeda, Dayna Terrazas, Pei-Yu Fu, Allen