Mechanism of action and therapeutic route for a muscular dystrophy caused by a genetic defect in lipid metabolism
由脂质代谢基因缺陷引起的肌营养不良症的作用机制和治疗途径
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-022-29270-z
Mahtab Tavasoli ,Sarah Lahire ,Stanislav Sokolenko ,Robyn Novorolsky ,Sarah Anne Reid ,Abir Lefsay ,Meredith O C Otley ,Kitipong Uaesoontrachoon ,Joyce Rowsell ,Sadish Srinivassane ,Molly Praest ,Alexandra MacKinnon ,Melissa Stella Mammoliti ,Ashley Alyssa Maloney ,Marina Moraca ,J Pedro Fernandez-Murray ,Meagan McKenna ,Christopher J Sinal ,Kanneboyina Nagaraju ,George S Robertson ,Eric P Hoffman ,Christopher R McMaster