Mutation-Specific Guide RNA for Compound Heterozygous Porphyria On-target Scarless Correction by CRISPR/Cas9 in Stem Cells
针对复合杂合卟啉症的突变特异性引导 RNA 通过干细胞中的 CRISPR/Cas9 进行靶向无瘢痕矫正
期刊:Stem Cell Reports
影响因子:5.9
doi:10.1016/j.stemcr.2020.07.015
Florence Prat, Jérôme Toutain, Julian Boutin, Samuel Amintas, Grégoire Cullot, Magalie Lalanne, Isabelle Lamrissi-Garcia, Isabelle Moranvillier, Emmanuel Richard, Jean-Marc Blouin, Sandrine Dabernat, François Moreau-Gaudry, Aurélie Bedel
