日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Disruption of HIV-1 co-receptors CCR5 and CXCR4 in primary human T cells and hematopoietic stem and progenitor cells using base editing

利用碱基编辑破坏人类原代 T 细胞和造血干细胞及祖细胞中的 HIV-1 辅助受体 CCR5 和 CXCR4

Friederike Knipping, Gregory A Newby, Cindy R Eide, Amber N McElroy, Sarah C Nielsen, Kyle Smith, Yongxing Fang, Tatjana I Cornu, Caroline Costa, Alejandra Gutierrez-Guerrero, Samuel P Bingea, Colby J Feser, Benjamin Steinbeck, Keli L Hippen, Bruce R Blazar, Anton McCaffrey, Claudio Mussolino, Els V

Correction of Fanconi Anemia Mutations Using Digital Genome Engineering

利用数字基因组工程技术纠正范可尼贫血症突变

Christopher J Sipe ,Mitchell G Kluesner ,Samuel P Bingea ,Walker S Lahr ,Aneesha A Andrew ,Minjing Wang ,Anthony P DeFeo ,Timothy L Hinkel ,Kanut Laoharawee ,John E Wagner ,Margaret L MacMillan ,Gregory M Vercellotti ,Jakub Tolar ,Mark J Osborn ,R Scott McIvor ,Beau R Webber ,Branden S Moriarity

CRISPR-Cas9 cytidine and adenosine base editing of splice-sites mediates highly-efficient disruption of proteins in primary and immortalized cells

CRISPR-Cas9 对剪接位点的胞嘧啶和腺苷碱基编辑可高效破坏原代细胞和永生化细胞中的蛋白质。

Mitchell G Kluesner # ,Walker S Lahr # ,Cara-Lin Lonetree ,Branden A Smeester ,Xiaohong Qiu ,Nicholas J Slipek ,Patricia N Claudio Vázquez ,Samuel P Pitzen ,Emily J Pomeroy ,Madison J Vignes ,Samantha C Lee ,Samuel P Bingea ,Aneesha A Andrew ,Beau R Webber ,Branden S Moriarity