日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cardiotropic AAV gene therapy for heart failure: a phase 1 trial

针对心力衰竭的心脏靶向性AAV基因疗法:一项I期试验

Henry, Timothy D; Chung, Eugene S; Alvisi, Monica; Sethna, Ferzin; Murray, David R; Traverse, Jay H; Roessig, Lothar; Roberts, Luke; Reddy, Swarna; Chen, Youjun; Ozkan, Tugba Guven; Webb, Stacy; Mittal, Monika; Ervin, Leigh; Sadek, Hesham; Mikhail, Sheila; Haghighi, Kobra; Jiang, Canwen; Samulski, R Jude; Kranias, Evangelia G; Tretiakova, Anna P; Hajjar, Roger J

New hope for older SMA patients with next-generation self-complementary AAV gene therapy

新一代自互补AAV基因疗法为老年SMA患者带来新希望

Nakai, Hiroyuki; Finanger, Erika L; Samulski, Richard Jude

AAV vector development, back to the future

AAV载体开发,回到未来

Suarez-Amaran, Lester; Song, Liujiang; Tretiakova, Anna P; Mikhail, Sheila A; Samulski, Richard Jude

Physical Activity for Anxiety for Autistic People: A Systematic Review

体育活动对自闭症患者焦虑的影响:系统性综述

Riis, Kathryn; Samulski, Brittany; Neely, Kristina A; Laverdure, Patricia

Rationally engineered novel AAV capsids for intra-articular gene delivery

合理设计的新型AAV衣壳用于关节内基因递送

Li, Wenjun; Feng, Susi Liu; Herrschaft, Lizette; Samulski, R Jude; Li, Chengwen

Primary peritoneal clear cell carcinoma arising in the setting of abdominal wall Endometriosis: A case report and review of the literature

原发性腹膜透明细胞癌发生于腹壁子宫内膜异位症背景下:病例报告及文献复习

Harris, Cameron M; Singleton, Miller P; Samulski, Theresa; Clark, Leslie H

Nicholas Muzyczka, PhD

尼古拉斯·穆齐奇卡博士

Berns, Kenneth I; Byrne, Barry J; Flotte, Terence R; Samulski, R Jude; Srivastava, Arun

Direct Comparison of Epifluorescence and Immunostaining for Assessing Viral Mediated Gene Expression in the Primate Brain

直接比较落射荧光法和免疫染色法在评估灵长类动物脑内病毒介导的基因表达中的应用

Tierney B Daw ,Hala G El-Nahal ,Michele A Basso ,Elizabeth J Jun ,Alex R Bautista ,R Jude Samulski ,Marc A Sommer ,Martin O Bohlen

Evaluation of an AAV9-mini-dystrophin gene therapy candidate in a rat model of Duchenne muscular dystrophy

对杜氏肌营养不良症大鼠模型中 AAV9-mini-dystrophin 基因治疗候选药物的评估

Caroline Le Guiner, Xiao Xiao, Thibaut Larcher, Aude Lafoux, Corinne Huchet, Gilles Toumaniantz, Oumeya Adjali, Ignacio Anegon, Séverine Remy, Josh Grieger, Juan Li, Vahid Farrokhi, Hendrik Neubert, Jane Owens, Maritza McIntyre, Philippe Moullier, R Jude Samulski

Customized blood-brain barrier shuttle peptide to increase AAV9 vector crossing the BBB and augment transduction in the brain

定制血脑屏障穿梭肽可增加 AAV9 载体穿越血脑屏障并增强脑内转导

Xintao Zhang, Zheng Chai, Amanda Lee Dobbins, Michelle S Itano, Charles Askew, Zhe Miao, Hongqian Niu, R Jude Samulski, Chengwen Li