日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cardiotropic AAV gene therapy for heart failure: a phase 1 trial

针对心力衰竭的心脏靶向性AAV基因疗法:一项I期试验

Henry, Timothy D; Chung, Eugene S; Alvisi, Monica; Sethna, Ferzin; Murray, David R; Traverse, Jay H; Roessig, Lothar; Roberts, Luke; Reddy, Swarna; Chen, Youjun; Ozkan, Tugba Guven; Webb, Stacy; Mittal, Monika; Ervin, Leigh; Sadek, Hesham; Mikhail, Sheila; Haghighi, Kobra; Jiang, Canwen; Samulski, R Jude; Kranias, Evangelia G; Tretiakova, Anna P; Hajjar, Roger J

Rationally engineered novel AAV capsids for intra-articular gene delivery

合理设计的新型AAV衣壳用于关节内基因递送

Li, Wenjun; Feng, Susi Liu; Herrschaft, Lizette; Samulski, R Jude; Li, Chengwen

Nicholas Muzyczka, PhD

尼古拉斯·穆齐奇卡博士

Berns, Kenneth I; Byrne, Barry J; Flotte, Terence R; Samulski, R Jude; Srivastava, Arun

Gene therapy approaches for equine osteoarthritis

马骨关节炎的基因治疗方法

Thampi, Parvathy; Samulski, R Jude; Grieger, Joshua C; Phillips, Jennifer N; McIlwraith, C Wayne; Goodrich, Laurie R

Corrigendum: Gene therapy approaches for equine osteoarthritis

勘误表:马骨关节炎的基因治疗方法

Thampi, Parvathy; Samulski, R Jude; Grieger, Joshua C; Phillips, Jennifer N; McIlwraith, C Wayne; Goodrich, Laurie R

BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression

BAX 335 B型血友病基因治疗临床试验结果:CpG序列对基因表达的潜在影响

Konkle, Barbara A; Walsh, Christopher E; Escobar, Miguel A; Josephson, Neil C; Young, Guy; von Drygalski, Annette; McPhee, Scott W J; Samulski, R Jude; Bilic, Ivan; de la Rosa, Maurus; Reipert, Birgit M; Rottensteiner, Hanspeter; Scheiflinger, Friedrich; Chapin, John C; Ewenstein, Bruce; Monahan, Paul E

"D" matters in recombinant AAV DNA packaging

在重组AAV DNA包装中,“D”很重要

Zhang, Junping; Guo, Ping; Xu, Yinxia; Mulcrone, Patrick L; Samulski, R Jude; Xiao, Weidong

Flies in the ointment: AAV vector preparations and tumor risk

美中不足的是:AAV载体制剂与肿瘤风险

Zhang, Junping; Yu, Xiangping; Herzog, Roland W; Samulski, R Jude; Xiao, Weidong

AAV Capsid-Promoter Interactions Determine CNS Cell-Selective Gene Expression In Vivo

AAV衣壳-启动子相互作用决定体内中枢神经系统细胞选择性基因表达

Powell, Sara K; Samulski, R Jude; McCown, Thomas J

Bound Protein- and Peptide-Based Strategies for Adeno-Associated Virus Vector-Mediated Gene Therapy: Where Do We Stand Now?

基于结合蛋白和肽的腺相关病毒载体介导基因治疗策略:我们现在处于什么阶段?

Zhang, Xintao; Chai, Zheng; Samulski, R Jude; Li, Chengwen