Preventing vision loss in a mouse model of Leber Congenital Amaurosis by engineered tRNA
利用基因工程改造的tRNA预防Leber先天性黑蒙小鼠模型的视力丧失
期刊:
影响因子:
doi:10.1101/2025.07.10.660754
Akyuz, Enes; Shahi, Pawan K; Gissot, Lionel; Saneh, Ahmad Al; Sinha, Divya; Hanstad, Giovanni M; Kabra, Meha; Zepeda, Maria A Fernandez; Gamm, David M; Young, Samuel M; Ahern, Christopher A; Pattnaik, Bikash R