日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

The European CAR-T map-Current status and future directions to improve access to CAR T-cell therapy for hematologic malignancies

欧洲CAR-T细胞疗法图谱——改善血液系统恶性肿瘤CAR-T细胞疗法可及性的现状与未来方向

Pennings, Elise R A; Thielen, Frederick W; Broussais, Florence; Delgado, Julio; Jaeger, Ulrich; Sanges, Carmen; Cabrerizo, Yolanda; Roux-Opstaele, Lutgart; Dreuillet, Caroline; Gonzalez-Marcano, Eglys; Millán, Olga; Huber, Barbara; Clavreul, Solène; Bolaños, Natacha; Nier, Samantha; Mihályová, Jana; Hájek, Roman; Horňáková, Michaela; Doeswijk, Robin; Thieblemont, Catherine; Hudecek, Michael; Uyl-de Groot, Carin A; Kersten, Marie José

Management of pulmonary arterial hypertension in systemic sclerosis: from classical treatments to new horizons

系统性硬化症肺动脉高压的治疗:从传统疗法到新方向

Villa, Annalisa; Sanges, Sébastien; Sobanski, Vincent; Lamblin, Nicolas; Rosato, Edoardo; Godinas, Laurent; Hachulla, Eric; Delcroix, Marion; Montani, David; Launay, David

Clinicopathological Spectrum and Treatment Outcomes of Cryofibrinogen-Associated Nephropathies

冷纤维蛋白原相关性肾病的临床病理谱和治疗结果

Dang, Julien; Faguer, Stanislas; Jourde-Chiche, Noémie; Javaugue, Vincent; Bridoux, Frank; Puissant, Bénédice; Heim, Xavier; Boffa, Jean-Jacques; François, Hélène; Tamzali, Yanis; Pillebout, Evangéline; Daugas, Eric; Monteiro, Renato; Daniel, Laurent; Chevalier, Kévin; Audard, Vincent; Van Wynsberghe, Margaux; Guerrot, Dominique; Legendre, Mathieu; Sanges, Sébastien; Lebas, Céline; Florens, Nans; Ronsin, Charles; Mussini, Charlotte; Ferlicot, Sophie; Mouawad, Sarah; Snanoudj, Renaud; Pimentel, Ana; Essig, Marie; De Chambrun, Marc Pineton; Ghillani-Dalbin, Pascale; Terrier, Benjamin; Zaidan, Mohamad

New insights into neurodevelopmental disorders by whole genome sequencing of 100 families from Italy

通过对意大利100个家庭进行全基因组测序,为神经发育障碍的研究提供了新的见解。

Spirito, Giovanni; Trova, Sara; Treves, Gaia; Farmanli, Khudayar; Canonico, Mariacristina Franzese; Fant, Agata; Marangoni, Stefano; Furia, Federica; Charrance, Debora; Locci, Nicola; Gottardo, Sara; Groppo, Francesca; Perseghin, Vittoria; Toscano, Martina; Bibbò, Erika; Dontin, Serena Donetti; Cargnelutti, Cecilia; Colliard, Mélody; Rosina, Alessandro; Beoni, Anna Maria; Bérard, Cristina; Coppe, Alessandro; Serravalle, Paolo; Landuzzi, Fabio; Musacchia, Francesco; Amoroso, Antonio; Sanges, Remo; Cavalli, Andrea; Vecchi, Manuela; Obino, Laure; Gustincich, Stefano

Is hereditary angioedema associated with deficits in emotion regulation? A quantitative study in adult patients

遗传性血管性水肿是否与情绪调节缺陷有关?一项针对成年患者的定量研究

Duprez, Christelle; Christophe, Véronique; Citerne, Isabelle; Raguet, Michel; Richez, Louise; Sanges, Sébastien; Launay, David

Berotralstat effectiveness and safety in patients with hereditary angioedema with normal C1 inhibitor

贝罗曲司他治疗C1抑制剂正常的遗传性血管性水肿患者的有效性和安全性

Buckland, Matthew S; Boccon-Gibod, Isabelle; De Moreuil, Claire; Sanges, Sébastien

Internal ribosome entry sites enhance translation in trans in antisense non-coding SINEUP and circular RNAs.

内部核糖体进入位点增强反义非编码 SINEUP 和环状 RNA 的反式翻译

D'Agostino Sabrina, Tettey-Matey Abraham, Volpe Massimiliano, Pierattini Bianca, D'Agostino Mattia, Smělá Denisa, Ansaloni Federico, Broglia Laura, Lau Pierre, Peruzzo Omar, Braccia Clarissa, Armirotti Andrea, Scarpato Margherita, Damiani Devid, Ros Gloria, Di Carlo Valerio, Maniscalco Federica, Bechara Elias, Tartaglia Gian Gaetano, Carninci Piero, Santoro Claudio, Persichetti Francesca, Pandolfini Luca, Simonetti Angelita, Espinoza Stefano, Zucchelli Silvia, Sanges Remo, Bon Carlotta, Gustincich Stefano

Optimizing CAR-T treatment: A T(2)EVOLVE guide to raw and starting material selection

优化 CAR-T 治疗:AT(2)EVOLVE 原料和起始材料选择指南

Navarro, Sergio; Moukheiber, Carole; Inogés Sancho, Susana; Ruiz Guillén, Marta; López-Díaz de Cerio, Ascensión; Sanges, Carmen; Tanaka, Toshimitsu; Arnould, Sylvain; Briones, Javier; Dolstra, Harry; Hudecek, Michael; Choudhary, Rashmi; Schapitz, Inga; Juan, Manel; Worel, Nina; Ammar, Delphine; Luu, Maik; Müller, Mirko; Schroeder, Bernd; Negre, Hélène; Franz, Paul

De novo and inherited variants in DDX39B cause a novel neurodevelopmental syndrome

DDX39B基因的新生突变和遗传突变会导致一种新的神经发育综合征。

Booth, Kevin T A; Jangam, Sharayu V; Chui, Martin M C; Treat, Kayla; Graziani, Lorenzo; Soldano, Alessia; Ruan, Yao; Wan-Hei Hui, Jeffrey; White, Kerry; Christensen, Celanie K; Lynnes, Ty; Yamamoto, Shinya; Kanca, Oguz; Tsang, Mandy H Y; Lynch, Sally A; Mullegama, Sureni V; Baptista, Julia; Iancu, Daniela; Joss, Shelagh K; Wong, Sandra Y Y; Mak, Christopher C Y; Kwong, Anna K Y; Bellen, Hugo J; Conboy, Erin; Sanges, Remo; Leung, Anskar Yu-Hung; Wangler, Michael F; Chung, Brian H Y; Vetrini, Francesco

A data management system for precision medicine

精准医疗数据管理系统

Jacobs, John J L; Beekers, Inés; Verkouter, Inge; Richards, Levi B; Vegelien, Alexandra; Bloemsma, Lizan D; Bongaerts, Vera A M C; Cloos, Jacqueline; Erkens, Frederik; Gradowska, Patrycja; Hort, Simon; Hudecek, Michael; Juan, Manel; Maitland-van der Zee, Anke H; Navarro-Velázquez, Sergio; Ngai, Lok Lam; Rafiq, Qasim A; Sanges, Carmen; Tettero, Jesse; van Os, Hendrikus J A; Vos, Rimke C; de Wit, Yolanda; van Dijk, Steven