Efficacy of Acoramidis in Wild-Type and Variant Transthyretin Amyloid Cardiomyopathy: Results From ATTRibute-CM and Its Open-Label Extension
Acoramidis治疗野生型和变异型转甲状腺素蛋白淀粉样变性心肌病的疗效:来自ATTRibute-CM及其开放标签扩展研究的结果
期刊:Jama Cardiology
影响因子:14.1
doi:10.1001/jamacardio.2025.4477
Alexander, Kevin M; Davis, Margot K; Akinboboye, Olakunle; Berk, John; Bhatt, Kunal; Cappelli, Francesco; Cuddy, Sarah A M; Fontana, Marianna; Garcia-Pavia, Pablo; Gillmore, Julian D; Griffin, Jan M; Grodin, Justin L; Judge, Daniel P; Khouri, Michel G; Lam, Kaitlyn; Masri, Ahmad; Maurer, Mathew S; Obici, Laura; Ruberg, Frederick L; Sarswat, Nitasha; Shah, Keyur; Soman, Prem; Stern, Lily; Wright, Richard; Xiong, Kuangnan; Cao, Xiaofan; Lystig, Ted; Tamby, Jean-François; Castaño, Adam; Katz, Leonid; Sinha, Uma; Fox, Jonathan C; Solomon, Scott D; Grogan, Martha