Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells
在患者来源的肝细胞样细胞中对家族性淀粉样多发性神经病的治疗性寡核苷酸进行评估
期刊:PLoS One
影响因子:2.9
doi:10.1371/journal.pone.0161455
Christoph J Niemietz, Vanessa Sauer, Jacqueline Stella, Lutz Fleischhauer, Gursimran Chandhok, Sarah Guttmann, Yesim Avsar, Shuling Guo, Elizabeth J Ackermann, Jared Gollob, Brett P Monia, Andree Zibert, Hartmut H-J Schmidt