Safety and biodistribution of intrathecal administration of mesenchymal stem cells (MSCs) and neurotrophin-releasing nanoparticles in a porcine CSF-guided delivery model for amyotrophic lateral sclerosis (ALS) drug discovery.
在猪脑脊液引导递送模型中,间充质干细胞 (MSC) 和神经营养因子释放纳米颗粒鞘内注射的安全性和生物分布,用于肌萎缩侧索硬化症 (ALS) 药物发现。
期刊:Scientific Reports
影响因子:3.9
doi:10.1038/s41598-026-40196-0
Sinderewicz Emilia, DÄ bkowska Maria, Sarnowska Anna, Staszkiewicz-Chodor Joanna, Mystkowska Dorota, Holak Piotr, Drozd Igor, Chodkowska-Michalowska Magdalena, Rytel Monika, Paczkowska Edyta, Mycko Marcin P, Machalinski Boguslaw, Jezierska-Wozniak Katarzyna