Preclinical assessment of GNE(wt)/bi-shRNA-GNE(M743T) lipoplex product development for GNE myopathy
GNE(wt)/bi-shRNA-GNE(M743T)脂质体复合物产品开发治疗GNE肌病的临床前评估
期刊:Future Science OA
影响因子:2.1
doi:10.1080/20565623.2026.2635722
Kerneis, Fabienne; Jay, Christopher M; Rao, Donald; Winchester, Jeremy; Nemunaitis, Alexander; Nemunaitis, Emily; Bognar, Ernest; Wallraven, Gladice; Stanbery, Laura; Walter, Adam; Sarshar, Sep; Nemunaitis, John