Patient-reported, psychosocial and health economic outcomes in mild to moderate Friedreich's ataxia: baseline results of the PROFA study
轻度至中度弗里德赖希共济失调患者的患者报告心理社会和健康经济学结果:PROFA 研究的基线结果
期刊:Lancet Regional Health-Europe
影响因子:13
doi:10.1016/j.lanepe.2025.101552
Grobe-Einsler, Marcus; Borel, Stéphanie; Buchholz, Maresa; Sayah, Sabrina; Hilab, Rania; Pierron, Lucie; Iskandar, Audrey; Humphries, Brittany; Ewenczyk, Claire; Heinzmann, Anna; Atencio, Mariana; Feldmann, Katrin; Maas, Vivian; Faber, Jennifer; Boesch, Sylvia; Indelicato, Elisabetta; Reetz, Kathrin; Schulz, Jörg B; Bischoff, Almut T; Klopstock, Thomas; Schöls, Ludger; Minnerop, Martina; Timmann, Dagmar; Davies, Elin H; Klockgether, Thomas; Durr, Alexandra; Xie, Feng; Michalowsky, Bernhard