日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Respiratory pathology in the mdx/utrn -/- mouse: A murine model for Duchenne Muscular Dystrophy (DMD).

mdx/utrn -/- 小鼠的呼吸病理学:杜氏肌营养不良症 (DMD) 的小鼠模型

Hernández Rodríguez Marán Y, Biswas Debolina D, Slyne Aoife D, Lee Jane, Scarrow Evelyn, Abdelbarr Sarra M, Daniels Heather, O'Halloran Ken D, Ferreira Leonardo F, Gersbach Charles A, ElMallah Mai K

GAA replacement improves respiratory muscle, neural, and alveolar pathology in the pompe mouse.

GAA 替代疗法可改善庞贝氏症小鼠的呼吸肌、神经和肺泡病理

Roger Angela L, El Haddad Lea, Huston Meredith L, Kehoe Sean, Le Davina, Khan Mainur, Scarrow Evelyn, Gonzalez Trevor, Benkert Abigail, Asokan Aravind, ElMallah Mai K

What's new and what's next for gene therapy in Pompe disease?

庞贝氏症基因治疗领域有哪些新进展和下一步发展方向?

Roger, Angela L; Sethi, Ronit; Huston, Meredith L; Scarrow, Evelyn; Bao-Dai, Joy; Lai, Elias; Biswas, Debolina D; El Haddad, Léa; Strickland, Laura M; Kishnani, Priya S; ElMallah, Mai K