日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Lucerastat, an oral therapy for Fabry disease: results from a pivotal randomized phase 3 study and its open-label extension

Lucerastat,一种用于治疗法布里病的口服药物:一项关键性随机3期研究及其开放标签扩展研究的结果

Nordbeck, Peter; Goker-Alpan, Ozlem; Bernat, John A; Germain, Dominique P; Giraldo, Pilar; Jovanovic, Ana; Kimonis, Virginia; Nicholls, Kathleen; Rockman-Greenberg, Cheryl; Schiffmann, Raphael; Thomas, Mark; Tylki-Szymanska, Anna; Wallace, Eric; Welford, Richard W D; West, Michael L; Clozel, Martine; Frey, Aline; Trokan, Luba; Mueller, Markus S; Vogler, Markus; Wanner, Christoph; Hughes, Derralynn

Oxidized MIF is an Alzheimer's disease drug target relaying external risk factors to tau pathology

氧化型MIF是阿尔茨海默病药物靶点,它将外部风险因素传递给tau蛋白病理。

Andreas Müller-Schiffmann,Felix Torres,Anatoliy Kitaygorodskyy,Anand Ramani,Argyro Alatza,Sarah K Tschirner,Julien Orts,Arthur Haltrich,Ingrid Prikulis,Shaofeng Yu,Debendranath Dey,Suguna Mallesh,Dharma Prasad,Dennis Solas,Verian Bader,Annemieke Rozemuller,Selina Wray,Jay Gopalakrishnan,Roland Riek,Vishwanath R Lingappa,Carsten Korth

Immune cell clustering identifies a CD163⁺/CSF1R⁺ macrophage and neutrophil-enriched phenotype with distinct biological signatures and poor prognosis in angiosarcoma

免疫细胞聚类分析可识别出一种富含CD163⁺/CSF1R⁺巨噬细胞和中性粒细胞的表型,该表型具有独特的生物学特征,且在血管肉瘤中预后不良。

Simon, Adrian Georg; Grothey, Bastian; Lyu, Su Ir; Stahl, David; Schiffmann, Lars Mortimer; Bruns, Christiane Josephine; Eysel, Peer; Buettner, Reinhard; Ullrich, Roland Tillmann; Quaas, Alexander

Age, Low Immunoglobulin G, and M Serum Levels Predict Infections in People With AQP4-IgG+ NMOSD Treated With Rituximab-A Multicenter Cohort Study From the German Neuromyelitis Optica Study Group (NEMOS)

年龄、低免疫球蛋白 G 和 M 血清水平可预测接受利妥昔单抗治疗的 AQP4-IgG+ NMOSD 患者的感染——来自德国视神经脊髓炎研究组 (NEMOS) 的一项多中心队列研究

Engels, Daniel; Herfurth, Mariella; Havla, Joachim; Schindler, Patrick; Ruprecht, Klemens; Schwake, Carolin; Ringelstein, Marius; Fischer, Katinka; Schubert, Charlotte; Schiffmann, Insa; Hümmert, Martin W; Giglhuber, Katrin; Jarius, Sven; Vardakas, Ioannis; Grothe, Matthias; Etgen, Thorleif; Warnke, Clemens; Naumann, Jasmin; Hoffmann, Frank; Senel, Makbule; Wildemann, Brigitte; Berthele, Achim; Trebst, Corinna; Häußler, Vivien; Aktas, Orhan; Ayzenberg, Ilya; Bellmann-Strobl, Judith; Bergh, Florian Then; Kümpfel, Tania

Schlafen 11 as a prognostic and potentially predictive biomarker in soft tissue sarcoma: evidence from a real-world cohort

Schlafen 11 作为软组织肉瘤的预后和潜在预测生物标志物:来自真实世界队列的证据

Simon, Adrian Georg; Lyu, Su Ir; Stahl, David; Schiffmann, Lars Mortimer; Wenk, Birte; Buettner, Reinhard; Wuerdemann, Nora; Tuchscherer, Armin; Ullrich, Roland Tillmann; Quaas, Alexander

PTPN1-related autoinflammation is a common cause of Aicardi-Goutières Syndrome with reduced penetrance

PTPN1相关的自身炎症是低外显率Aicardi-Goutières综合征的常见病因

Calame, Daniel G; Wiener, Emma K; Gavazzi, Francesco; Sevagamoorthy, Anjana; Pizzino, Amy; Arnold, Kaley; Dominguez Gonzalez, Carlos; Jammihal, Tejas; Bennett, Mariko; Adang, Laura; Woidill, Sarah; Whitehead, Matthew T; Vossough, Arastoo; D'Aiello, Russell; Takanohashi, Asako; Lele, Janhavi; Simons, Cas; Rius, Rocio; Formaini, Edward; Sullivan, Kathleen E; Andzelm, Milena; Ebrahimi-Fakhari, Darius; Otten, Catherine; Wong, Stephen; Reynolds, Thomas; Schiffmann, Raphael; Wolf, Nicole I; Waisfisz, Quinten; Niermeijer, Jikke-Mien; DeMarzo, Danielle; Dawood, Moez; Gandhi, Mira; Levine, Jesse M; Chinn, Ivan K; Fisher, Kristen; Emrick, Lisa; Alam, Chadi Al; Kaiyrzhanov, Rauan; Maroofian, Reza; Houlden, Henry; Jhangiani, Shalini N; Mehta, Heer H; Muzny, Donna M; Sedlazeck, Fritz J; Posey, Jennifer E; Lupski, James R; Gibbs, Richard A; Rajagopalan, Ramakrishnan; Vanderver, Adeline

Therapeutic Fasting as a Novel Approach to Mitigate Musculoskeletal Symptoms in Breast Cancer Patients undergoing Aromatase Inhibitor Therapy: A Feasibility Study Protocol

治疗性禁食作为一种缓解接受芳香化酶抑制剂治疗的乳腺癌患者肌肉骨骼症状的新方法:一项可行性研究方案

Meyer, Henriette; Koppold, Daniela A; Shaker, Osaid; Eden, Laura; Schiffmann, Lisa; Konigorski, Stefan; Cramer, Holger; Choi, Kyung-Eun Anna; Einsele, Hermann; Winkler, Marcela; Löffler, Claudia

Zoos must embrace animal death for education and conservation

动物园必须接受动物死亡,将其用于教育和保护目的。

Clauss, Marcus; Roller, Marco; Bertelsen, Mads Frost; Rudolf von Rohr, Claudia; Müller, Dennis W H; Schiffmann, Christian; Kummrow, Maya; Encke, Dag; Ferreira, Sam; Duvall, Ethan S; Maré, Celesté; Abraham, Andrew J

Reply to Ferraro et al.: Breed-and-feed reflects inevitable trade-offs between individual longevity and population sustainability

回复 Ferraro 等人:繁殖和饲养反映了个体寿命和种群可持续性之间不可避免的权衡。

Clauss, Marcus; Roller, Marco; Bertelsen, Mads F; Rudolf von Rohr, Claudia; Müller, Dennis W H; Schiffmann, Christian; Kummrow, Maya; Encke, Dag; Ferreira, Sam; Duvall, Ethan S; Maré, Celesté; Abraham, Andrew J

Real-world multicentre cohort study on choices and effectiveness of immunotherapies in NMOSD and MOGAD

一项关于视神经脊髓炎谱系障碍 (NMOSD) 和髓鞘少突胶质细胞抗原缺乏症 (MOGAD) 免疫疗法选择和疗效的真实世界多中心队列研究

Häußler, Vivien; Trebst, Corinna; Engels, Daniel; Pellkofer, Hanna; Havla, Joachim; Duchow, Ankelien; Schindler, Patrick; Schwake, Carolin; Pakeerathan, Thivya; Fischer, Katinka; Ringelstein, Marius; Lindenblatt, Gero; Hümmert, Martin W; Tkachenko, Daria; Bütow, Franziska; Giglhuber, Katrin; Flaskamp, Martina; Schiffmann, Insa; Korporal-Kuhnke, Mirjam; Jarius, Sven; Dawin, Eva; Revie, Lisa; Senel, Makbule; Herfurth, Mariella; Walter, Annette; Pompsch, Mosche; Kleiter, Ingo; Angstwurm, Klemens; Kaste, Matthias; Grothe, Matthias; Wickel, Jonathan; Rommer, Paulus Stefan; Sieb, Jörn Peter; Krämer, Markus; Then Bergh, Florian; Tumani, Hayrettin; Klotz, Luisa; Wildemann, Brigitte; Aktas, Orhan; Ayzenberg, Ilya; Bellmann-Strobl, Judith; Paul, Friedemann; Kümpfel, Tania; Friede, Tim; Berthele, Achim; Stellmann, Jan-Patrick