日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

DNA-PKcs inhibitor AZD7648 reveals sgRNA cross-contaminants and enhanced sensitivity of genome engineering off-target activity in HSPCs

DNA-PKcs抑制剂AZD7648揭示了sgRNA交叉污染,并增强了造血干细胞中基因组工程脱靶活性的敏感性

White, Nathan; Hu, Yi-Ting; Chalk, John Alexander; Kurgan, Gavin; Naseem, Asma; Schmaljohn, Ellen; Sturgeon, Morgan; Cavazza, Alessia; Thrasher, Adrian James; Turchiano, Giandomenico

Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease

利用患者特异性体内基因编辑技术治疗罕见遗传疾病

Musunuru, Kiran; Grandinette, Sarah A; Wang, Xiao; Hudson, Taylor R; Briseno, Kevin; Berry, Anne Marie; Hacker, Julia L; Hsu, Alvin; Silverstein, Rachel A; Hille, Logan T; Ogul, Aysel N; Robinson-Garvin, Nancy A; Small, Juliana C; McCague, Sarah; Burke, Samantha M; Wright, Christina M; Bick, Sarah; Indurthi, Venkata; Sharma, Shweta; Jepperson, Michael; Vakulskas, Christopher A; Collingwood, Michael; Keogh, Katie; Jacobi, Ashley; Sturgeon, Morgan; Brommel, Christian; Schmaljohn, Ellen; Kurgan, Gavin; Osborne, Thomas; Zhang, He; Kinney, Kyle; Rettig, Garrett; Barbosa, Christopher J; Semple, Sean C; Tam, Ying K; Lutz, Cathleen; George, Lindsey A; Kleinstiver, Benjamin P; Liu, David R; Ng, Kim; Kassim, Sadik H; Giannikopoulos, Petros; Alameh, Mohamad-Gabriel; Urnov, Fyodor D; Ahrens-Nicklas, Rebecca C

Pathogenicity and virulence of Rodent-Borne Orthohantaviruses

啮齿类正汉坦病毒的致病性和毒力

Taylor, Shannon L; Schmaljohn, Connie S; Williams, Evan P; Jonsson, Colleen B

Annual (2024) taxonomic update of RNA-directed RNA polymerase-encoding negative-sense RNA viruses (realm Riboviria: kingdom Orthornavirae: phylum Negarnaviricota)

RNA 指导的 RNA 聚合酶编码负链 RNA 病毒的年度(2024 年)分类更新(核糖病毒域:正核病毒界:负链病毒门)

Kuhn, Jens H; Adkins, Scott; Alkhovsky, Sergey V; An, Wenxia; Avšič-Županc, Tatjana; Ayllón, María A; Bačnik, Katarina; Bahl, Justin; Balkema-Buschmann, Anne; Ballinger, Matthew J; Beer, Martin; Bejerman, Nicolas; Bergeron, Éric; Biedenkopf, Nadine; Blair, Carol D; Blasdell, Kim R; Bradfute, Steven B; Briese, Thomas; Brown, Katherine; Brown, Paul A; Buchholz, Ursula J; Buchmeier, Michael J; Bukreyev, Alexander; Burt, Felicity; Calisher, Charles H; Calvelage, Sten; Cao, Mengji; Casas, Inmaculada; Chabi-Jesus, Camila; Chandran, Kartik; Charrel, Rémi N; Crane, Anya; Cuypers, Laura N; Bó, Elena Dal; de la Torre, Juan Carlos; de Souza, William M; de Swart, Rik L; Debat, Humberto J; Dheilly, Nolwenn M; Di Paola, Nicholas; Di Serio, Francesco; Dietzgen, Ralf G; Digiaro, Michele; Drexler, J Felix; Duprex, W Paul; Dürrwald, Ralf; Easton, Andrew J; Elbeaino, Toufic; Ergünay, Koray; Eshak, Mirette I Y; Feng, Guozhong; Firth, Andrew E; Fooks, Anthony R; Formenty, Pierre B H; Freitas-Astúa, Juliana; Freuling, Conrad M; Gadd, Tuija; Gago-Zachert, Selma; García, María Laura; García-Sastre, Adolfo; Garrison, Aura R; Goldberg, Tony L; Gonzalez, Jean-Paul J; Goüy de Bellocq, Joëlle; Griffiths, Anthony; Groschup, Martin H; Gryseels, Sophie; Gutiérrez-Aguirre, Ion; Günther, Stephan; Hammond, John; Hepojoki, Jussi; Horie, Masayuki; Hume, Adam J; Hyndman, Timothy H; Höper, Dirk; Jiāng, Dàohóng; Junglen, Sandra; Klempa, Boris; Klingström, Jonas; Kondō, Hideki; Koonin, Eugene V; Krupovic, Mart; Kubota, Kenji; Kurath, Gael; Kutnjak, Denis; Laenen, Lies; Lambert, Amy J; Lee, Benhur; Li, Chengyu; Lǐ, Jiànróng; Li, Jun-Min; Lukashevich, Igor S; Maes, Piet; Marklewitz, Marco; Marshall, Sergio H; Marzano, Shin-Yi L; McCauley, John W; Mehle, Nataša; Mirazimi, Ali; Morikawa, Toshiyuki; Mühlberger, Elke; Müller, Thomas; Naidu, Rayapati; Natsuaki, Tomohide; Navarro, Beatriz; Navarro, José A; Neriya, Yutaro; Netesov, Sergey V; Nicoloso, Vittorio M; Neumann, Gabriele; Nokireki, Tiina; Nowotny, Norbert; Nunes, Márcio R T; Ochoa-Corona, Francisco M; Palacios, Gustavo; Pallás, Vicente; Papa, Anna; Paraskevopoulou, Sofia; Parrish, Colin R; Pauvolid-Corrêa, Alex; Pecman, Anja; Pérez, Daniel R; Pfaff, Florian; Plemper, Richard K; Postler, Thomas S; Radoshitzky, Sheli R; Ramos-González, Pedro L; Ravnikar, Maja; Resende, Renato O; Reuter, Gábor; Reyes, Carina A; Rivarez, Mark Paul Selda; Romanowski, Víctor; Rubbenstroth, Dennis; Rubino, Luisa; Runstadler, Jonathan A; Ruiz-Padilla, Ana; Sabanadzovic, Sead; Salvato, Maria S; Sasaya, Takahide; Schmaljohn, Connie S; Schmidt-Posthaus, Heike; Schwemmle, Martin; Seljak, Gabrijel; Seuberlich, Torsten; Shi, Mang; Shimomoto, Yoshifumi; Simmonds, Peter; Sironi, Manuela; Smith, Donald B; Smither, Sophie; Song, Jin-Won; Spann, Kirsten M; Spengler, Jessica R; Stenglein, Mark D; Takada, Ayato; Takemura, Chika; Tammiranta, Niina; Tesh, Robert B; Thornburg, Natalie J; Tischler, Nicole D; Tomitaka, Yasuhiro; Tomonaga, Keizō; Tordo, Noël; Turina, Massimo; Tzanetakis, Ioannis E; Vaira, Anna Maria; van den Hoogen, Bernadette; Vanmechelen, Bert; Vasilakis, Nikos; Verbeek, Martin; von Bargen, Susanne; Vučurović, Ana; Wada, Jiro; Wahl, Victoria; Walker, Peter J; Wang, Fei; Whitfield, Anna E; Williams, John V; Wolf, Yuri I; Yanagisawa, Hironobu; Yang, Caixia; Ye, Gongyin; Yu, Mei Chun; Zerbini, F Murilo; Zhang, Song; Økland, Arnfinn Lodden; Hughes, Holly R

HSP90 is part of a protein complex with the L polymerase of Rift Valley fever phlebovirus and prevents its degradation by the proteasome during the viral genome replication/transcription stage

HSP90 是裂谷热白蛉病毒 L 聚合酶的蛋白质复合物的一部分,可在病毒基因组复制/转录阶段防止蛋白酶体降解

Farhang Alem, Ashwini Brahms, Kaori Tarasaki, Samson Omole, Kylene Kehn-Hall, Connie S Schmaljohn, Sina Bavari, Shinji Makino, Ramin M Hakami

Characterization of therapeutic antibody efficacy against multiple SARS-CoV-2 variants in the hamster model

在仓鼠模型中表征治疗性抗体对多种SARS-CoV-2变异株的疗效

Cong, Yu; Dixit, Saurabh; Perry, Donna L; Huzella, Louis M; Kollins, Erin; Byrum, Russell; Anthony, Scott M; Drawbaugh, David; Lembirik, Sanae; Postnikova, Elena; Eaton, Brett; Murphy, Michael; Kocher, Gregory; Hadley, Kyra; Marketon, Anthony E; Bernbaum, Rebecca M; Hischak, Amanda M W; Hart, Randy; Vaughan, Nick; Wada, Jiro; Qin, Jing; St Claire, Marisa C; Schmaljohn, Connie S; Holbrook, Michael R

The DNA-based Lassa vaccine INO-4500 confers durable protective efficacy in cynomolgus macaques against lethal Lassa fever

基于 DNA 的拉沙疫苗 INO-4500 为猕猴提供持久的保护功效,防止其感染致命的拉沙热

Viviane M Andrade #, Kathleen Cashman #, Kyle Rosenke, Eric Wilkinson, Nicole Josleyn, Ginger Lynn, Jesse Steffens, Sean Vantongeren, Jay Wells, Connie Schmaljohn, Paul Facemire, Jingjing Jiang, Jean Boyer, Aditya Patel, Friederike Feldmann, Patrick Hanley, Jamie Lovaglio, Kimberly White, Heinz Feld

Rare, convergent antibodies targeting the stem helix broadly neutralize diverse betacoronaviruses

罕见的、趋同的抗体靶向茎螺旋结构,可广泛中和多种β冠状病毒

Cherrelle Dacon ,Linghang Peng ,Ting-Hui Lin ,Courtney Tucker ,Chang-Chun D Lee ,Yu Cong ,Lingshu Wang ,Lauren Purser ,Andrew J R Cooper ,Jazmean K Williams ,Chul-Woo Pyo ,Meng Yuan ,Ivan Kosik ,Zhe Hu ,Ming Zhao ,Divya Mohan ,Mary Peterson ,Jeff Skinner ,Saurabh Dixit ,Erin Kollins ,Louis Huzella ,Donna Perry ,Russell Byrum ,Sanae Lembirik ,Michael Murphy ,Yi Zhang ,Eun Sung Yang ,Man Chen ,Kwanyee Leung ,Rona S Weinberg ,Amarendra Pegu ,Daniel E Geraghty ,Edgar Davidson ,Benjamin J Doranz ,Iyadh Douagi ,Susan Moir ,Jonathan W Yewdell ,Connie Schmaljohn ,Peter D Crompton ,John R Mascola ,Michael R Holbrook ,David Nemazee ,Ian A Wilson ,Joshua Tan

Rare, convergent antibodies targeting the stem helix broadly neutralize diverse betacoronaviruses

罕见的、趋同的抗体靶向茎螺旋结构,可广泛中和多种β冠状病毒

Dacon, Cherrelle; Peng, Linghang; Lin, Ting-Hui; Tucker, Courtney; Lee, Chang-Chun D; Cong, Yu; Wang, Lingshu; Purser, Lauren; Cooper, Andrew J R; Williams, Jazmean K; Pyo, Chul-Woo; Yuan, Meng; Kosik, Ivan; Hu, Zhe; Zhao, Ming; Mohan, Divya; Peterson, Mary; Skinner, Jeff; Dixit, Saurabh; Kollins, Erin; Huzella, Louis; Perry, Donna; Byrum, Russell; Lembirik, Sanae; Murphy, Michael; Zhang, Yi; Yang, Eun Sung; Chen, Man; Leung, Kwanyee; Weinberg, Rona S; Pegu, Amarendra; Geraghty, Daniel E; Davidson, Edgar; Doranz, Benjamin J; Douagi, Iyadh; Moir, Susan; Yewdell, Jonathan W; Schmaljohn, Connie; Crompton, Peter D; Mascola, John R; Holbrook, Michael R; Nemazee, David; Wilson, Ian A; Tan, Joshua

Depletion of Bone Marrow Hematopoietic Cells in Ebolavirus-Infected Rhesus Macaques: A Possible Cause of Hematologic Abnormalities in Ebolavirus Disease

埃博拉病毒感染恒河猴骨髓造血细胞耗竭:埃博拉病毒病血液系统异常的可能原因

David X Liu ,Bapi Pahar ,Donna L Perry ,Huanbin Xu ,Timothy K Cooper ,Louis M Huzella ,Randy J Hart ,Amanda M W Hischak ,John Bernbaum ,Marisa St Claire ,Russell Byrum ,Richard S Bennett ,Travis Warren ,Michael R Holbrook ,Lisa E Hensley ,Ian Crozier ,Connie S Schmaljohn