CRISPR/Cas9-Correctable mutation-related molecular and physiological phenotypes in iPSC-derived Alzheimer's PSEN2 N141I neurons
iPSC 衍生的阿尔茨海默病 PSEN2 N141I 神经元中 CRISPR/Cas9 可校正突变相关分子和生理表型
期刊:Acta Neuropathologica Communications
影响因子:6.2
doi:10.1186/s40478-017-0475-z
Maitane Ortiz-Virumbrales, Cesar L Moreno, Ilya Kruglikov, Paula Marazuela, Andrew Sproul, Samson Jacob, Matthew Zimmer, Daniel Paull, Bin Zhang, Eric E Schadt, Michelle E Ehrlich, Rudolph E Tanzi, Ottavio Arancio, Scott Noggle, Sam Gandy2