Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity
生物工程改造的AAV衣壳,兼具体内高人肝转导效率和独特的体液血清反应性。
期刊:Molecular Therapy
影响因子:12.1
doi:10.1016/j.ymthe.2017.09.021
Nicole K Paulk ,Katja Pekrun ,Erhua Zhu ,Sean Nygaard ,Bin Li ,Jianpeng Xu ,Kirk Chu ,Christian Leborgne ,Allison P Dane ,Annelise Haft ,Yue Zhang ,Feijie Zhang ,Chris Morton ,Marcus B Valentine ,Andrew M Davidoff ,Amit C Nathwani ,Federico Mingozzi ,Markus Grompe ,Ian E Alexander ,Leszek Lisowski ,Mark A Kay