日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Therapeutic liver repopulation by transient acetaminophen selection of gene-modified hepatocytes

利用对乙酰氨基酚瞬时筛选基因修饰的肝细胞进行治疗性肝脏再生

Anne Vonada,Amita Tiyaboonchai,Sean Nygaard,Jeffrey Posey,Alexander Mack Peters,Shelley R Winn,Alessio Cantore,Luigi Naldini,Cary O Harding,Markus Grompe

Induced Liver Regeneration Enhances CRISPR/Cas9-Mediated Gene Repair in Tyrosinemia Type 1

诱导肝再生增强酪氨酸血症 1 型中的 CRISPR/Cas9 介导的基因修复

Qing-Shuo Zhang, Amita Tiyaboonchai, Sean Nygaard, Kevin Baradar, Angela Major, Niveditha Balaji, Markus Grompe

Using a barcoded AAV capsid library to select for clinically relevant gene therapy vectors

利用条形码标记的AAV衣壳文库筛选具有临床意义的基因治疗载体

Katja Pekrun ,Gustavo De Alencastro ,Qing-Jun Luo ,Jun Liu ,Youngjin Kim ,Sean Nygaard ,Feorillo Galivo ,Feijie Zhang ,Ren Song ,Matthew R Tiffany ,Jianpeng Xu ,Matthias Hebrok ,Markus Grompe ,Mark A Kay

Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity

生物工程改造的AAV衣壳,兼具体内高人肝转导效率和独特的体液血清反应性。

Nicole K Paulk ,Katja Pekrun ,Erhua Zhu ,Sean Nygaard ,Bin Li ,Jianpeng Xu ,Kirk Chu ,Christian Leborgne ,Allison P Dane ,Annelise Haft ,Yue Zhang ,Feijie Zhang ,Chris Morton ,Marcus B Valentine ,Andrew M Davidoff ,Amit C Nathwani ,Federico Mingozzi ,Markus Grompe ,Ian E Alexander ,Leszek Lisowski ,Mark A Kay

A universal system to select gene-modified hepatocytes in vivo

一种在体内选择基因修饰肝细胞的通用系统

Sean Nygaard, Adi Barzel, Annelise Haft, Angela Major, Milton Finegold, Mark A Kay, Markus Grompe

Selection and evaluation of clinically relevant AAV variants in a xenograft liver model

在异种移植肝模型中筛选和评估具有临床意义的AAV变体

Leszek Lisowski ,Allison P Dane ,Kirk Chu ,Yue Zhang ,Sharon C Cunningham ,Elizabeth M Wilson ,Sean Nygaard ,Markus Grompe ,Ian E Alexander ,Mark A Kay

Brain-derived neurotrophic factor activation of CaM-kinase kinase via transient receptor potential canonical channels induces the translation and synaptic incorporation of GluA1-containing calcium-permeable AMPA receptors

脑源性神经营养因子通过瞬时受体电位典型通道激活 CaM-激酶激酶,诱导含 GluA1 的钙通透性 AMPA 受体的翻译和突触整合

Dale A Fortin, Taasin Srivastava, Diya Dwarakanath, Philippe Pierre, Sean Nygaard, Victor A Derkach, Thomas R Soderling

Transient receptor potential canonical 5 channels activate Ca2+/calmodulin kinase Igamma to promote axon formation in hippocampal neurons

瞬时受体电位典型 5 通道激活 Ca2+/钙调蛋白激酶 Igamma 促进海马神经元轴突形成

Monika A Davare, Dale A Fortin, Takeo Saneyoshi, Sean Nygaard, Stefanie Kaech, Gary Banker, Thomas R Soderling, Gary A Wayman