日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

FORCE platform overcomes barriers of oligonucleotide delivery to muscle and corrects myotonic dystrophy features in preclinical models

FORCE 平台克服了寡核苷酸输送到肌肉的障碍,并纠正了临床前模型中的强直性肌营养不良症特征

Timothy Weeden, Tyler Picariello, Brendan Quinn, Sean Spring, Pei-Yi Shen, Qifeng Qiu, Benjamin F Vieira, Lydia Schlaefke, Ryan J Russo, Ya-An Chang, Jin Cui, Monica Yao, Aiyun Wen, Nelson Hsia, Tama Evron, Katy Ovington, Pei-Ni Tsai, Nicholas Yoder, Bo Lan, Reshmii Venkatesan, John Hall, Cody A Des

Enhanced exon skipping and prolonged dystrophin restoration achieved by TfR1-targeted delivery of antisense oligonucleotide using FORCE conjugation in mdx mice

在 mdx 小鼠中,使用 FORCE 结合技术向 TfR1 靶向递送反义寡核苷酸可增强外显子跳跃并延长肌营养不良蛋白的恢复时间

Cody A Desjardins, Monica Yao, John Hall, Emma O'Donnell, Reshmii Venkatesan, Sean Spring, Aiyun Wen, Nelson Hsia, Peiyi Shen, Ryan Russo, Bo Lan, Tyler Picariello, Kim Tang, Timothy Weeden, Stefano Zanotti, Romesh Subramanian, Oxana Ibraghimov-Beskrovnaya

Virus-Like Particle-Drug Conjugates Induce Protective, Long-lasting Adaptive Antitumor Immunity in the Absence of Specifically Targeted Tumor Antigens

病毒样颗粒-药物偶联物在缺乏特异性靶向肿瘤抗原的情况下诱导保护性、持久的适应性抗肿瘤免疫

Rhonda C Kines, Cynthia D Thompson, Sean Spring, Zhenyu Li, Elisabet de Los Pinos, Stephen Monks, John T Schiller