Gene correction of HBB mutations in CD34+ hematopoietic stem cells using Cas9 mRNA and ssODN donors
使用 Cas9 mRNA 和 ssODN 供体对 CD34+ 造血干细胞中的 HBB 突变进行基因校正
期刊:Molecular and Cellular Pediatrics
影响因子:2.4
doi:10.1186/s40348-018-0086-1
Justin S Antony, Ngadhnjim Latifi, A K M Ashiqul Haque, Andrés Lamsfus-Calle, Alberto Daniel-Moreno, Sebastian Graeter, Praveen Baskaran, Petra Weinmann, Markus Mezger, Rupert Handgretinger, Michael S D Kormann
