日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

In vivo adenine base editing reverts C282Y and improves iron metabolism in hemochromatosis mice

体内腺嘌呤碱基编辑可逆转 C282Y 并改善血色素沉着症小鼠的铁代谢

Alice Rovai, BoMee Chung, Qingluan Hu, Sebastian Hook, Qinggong Yuan, Tibor Kempf, Florian Schmidt, Dirk Grimm, Steven R Talbot, Lars Steinbrück, Jasper Götting, Jens Bohne, Simon A Krooss, Michael Ott

Hepatocellular Carcinoma Is a Natural Target for Adeno-Associated Virus (AAV) 2 Vectors

肝细胞癌是腺相关病毒 (AAV) 2 载体的天然靶点

Nadja Meumann, Christian Schmithals, Leroy Elenschneider, Tanja Hansen, Asha Balakrishnan, Qingluan Hu, Sebastian Hook, Jessica Schmitz, Jan Hinrich Bräsen, Ann-Christin Franke, Olaniyi Olarewaju, Christina Brandenberger, Steven R Talbot, Josef Fangmann, Ulrich T Hacker, Margarete Odenthal, Michael

Spatiotemporally confined red light-controlled gene delivery at single-cell resolution using adeno-associated viral vectors

利用腺相关病毒载体以单细胞分辨率进行时空受限的红光控制基因传递

Maximilian Hörner, Carolina Jerez-Longres, Anna Hudek, Sebastian Hook, O Sascha Yousefi, Wolfgang W A Schamel, Cindy Hörner, Matias D Zurbriggen, Haifeng Ye, Hanna J Wagner, Wilfried Weber