Investigation of New Morpholino Oligomers to Increase Survival Motor Neuron Protein Levels in Spinal Muscular Atrophy
研究新型吗啉代寡核苷酸以提高脊髓性肌萎缩症中存活运动神经元蛋白的水平
期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms19010167
Ramirez, Agnese; Crisafulli, Sebastiano G; Rizzuti, Mafalda; Bresolin, Nereo; Comi, Giacomo P; Corti, Stefania; Nizzardo, Monica