Antisense oligonucleotide therapy for KCNT1 encephalopathy
反义寡核苷酸治疗 KCNT1 脑病
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.146090
Lisseth Estefania Burbano, Melody Li, Nikola Jancovski, Paymaan Jafar-Nejad, Kay Richards, Alicia Sedo, Armand Soriano, Ben Rollo, Linghan Jia, Elena V Gazina, Sandra Piltz, Fatwa Adikusuma, Paul Q Thomas, Helen Kopsidas, Frank Rigo, Christopher A Reid, Snezana Maljevic, Steven Petrou