日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Longitudinal multi-omics profiling of spinal muscular atrophy

脊髓性肌萎缩症的纵向多组学分析

Dabaj, Ivana; Nguyen, Thi Hai Yen; Lagrue, Emmanuelle; Ducatez, Franklin; Allouche, Stéphane; Ausseil, Jérôme; Seferian, Andreea; Gomez-Garcia de la Banda, Marta; Benezit, Audrey; Phelep, Aurélie; Chouchane, Mondher; Vasseur, Stéphane; Chapart, Maud; Marret, Stéphane; Quijano Roy, Susana; Tebani, Abdellah; Bekri, Soumeya

Role of the HGF/c-MET pathway in resistance to immune checkpoint inhibitors in advanced non-small cell lung cancer

HGF/c-MET 通路在晚期非小细胞肺癌免疫检查点抑制剂耐药中的作用

Assya Akli #, Paul Takam Kamga #, Catherine Julie, Claude Capron, Adrien Costantini, Coraline Dumenil, Jennifer Dumoulin, Violaine Giraud, Florence Parent, Andrei Seferian, Catherine Guettier, Mathieu Glorion, Elisabeth Longchampt, Jean-François Emile, Étienne Giroux-Leprieur

Low-Cost System to Support and Expand Cyanobacterial Harmful Algal Bloom Monitoring with New-Generation Ocean Color Satellites

利用新一代海洋水色卫星支持和扩展蓝藻有害藻华监测的低成本系统

Maniyar, Chintan B; Raviprakash, Keshav; Kumar, Abhishek; Seferian, Mark A; Fiorentino, Isabella R; Mishra, Deepak R

The Safety Action Feedback and Engagement (SAFE) Loop: Initial Testing and Refinement of a Novel Intervention to Enhance Hospital Incident Reporting and Patient Safety

安全行动反馈与参与(SAFE)循环:一项旨在提升医院事故报告和患者安全的新型干预措施的初步测试与完善

Seferian, Edward; Berdahl, Carl T; Coleman, Bernice; Leang, Donna; Cohen, Tara; Qureshi, Nabeel; McCleskey, Sara G; Kaiser, Karen; Grissinger, Matthew; Kanji, Falisha; Henreid, Andrew J; Carrascoza-Bolanos, Johan; Daniels, Laura; Abarca, Oscar Jr; De La Cruz, Pamela; Truong, Brandon T; Nuckols, Teryl K

Gene therapy for children with X-linked myotubular myopathy: a plain language summary of publication for the ASPIRO study

针对患有 X 连锁肌管性肌病儿童的基因疗法:ASPIRO 研究出版物的通俗易懂的摘要

Shieh, Perry B; Hughes, Wendy; Wood, Marie; Beggs, Alan H; Lawlor, Michael W; Coats, Julie; Varfaj, Fatbardha; Graham, Robert J; Kuntz, Nancy L; Dowling, James J; Müller-Felber, Wolfgang; Bönnemann, Carsten G; Buj Bello, Ana; Servais, Laurent; MacBean, Vicky; Muntoni, Francesco; Foley, A Reghan; Blaschek, Astrid; James, Emma S; Seferian, Andreea; Alfano, Lindsay N; Duong, Tina; Noursalehi, Mojtaba; Miller, Weston; Lee, Jun; Prasad, Suyash; Rico, Salvador

Multi-omic analysis of the ciliogenic transcription factor RFX3 reveals a role in promoting activity-dependent responses via enhancing CREB binding in human neurons.

对纤毛生成转录因子 RFX3 的多组学分析揭示了其通过增强人类神经元中 CREB 结合来促进活动依赖性反应的作用

Lai Jenny, Demirbas Didem, Phillips Kaitlyn, Zhao Boxun, Wallace Harrison, Seferian Megan, Nakayama Tojo, Harris Holly, Chatzipli Aikaterini, Lee Eunjung Alice, Yu Timothy W

Effects of gene replacement therapy with resamirigene bilparvovec (AT132) on skeletal muscle pathology in X-linked myotubular myopathy: results from a substudy of the ASPIRO open-label clinical trial

使用 resamirigene bilparvovec (AT132) 进行基因替代疗法对 X 连锁肌管性肌病骨骼肌病理的影响:来自 ASPIRO 开放标签临床试验子研究的结果

Michael W Lawlor, Benedikt Schoser, Marta Margeta, Caroline A Sewry, Karra A Jones, Perry B Shieh, Nancy L Kuntz, Barbara K Smith, James J Dowling, Wolfgang Müller-Felber, Carsten G Bönnemann, Andreea M Seferian, Astrid Blaschek, Sarah Neuhaus, A Reghan Foley, Dimah N Saade, Etsuko Tsuchiya, Ummulwa

Characteristics and outcomes of gemcitabine-associated pulmonary hypertension

吉西他滨相关性肺动脉高压的特征和预后

Mouillot, Pierre; Favrolt, Nicolas; Khouri, Charles; Grandvuillemin, Aurélie; Chaumais, Marie-Camille; Schenesse, Déborah; Seferian, Andrei; Jais, Xavier; Savale, Laurent; Beltramo, Guillaume; Sitbon, Olivier; Cracowski, Jean-Luc; Humbert, Marc; Georges, Marjolaine; Bonniaud, Philippe; Montani, David

Outcomes and risk assessment in pulmonary veno-occlusive disease

肺静脉闭塞性疾病的预后和风险评估

Boucly, Athénaïs; Solinas, Sabina; Beurnier, Antoine; Jaïs, Xavier; Keddache, Sophia; Eyries, Mélanie; Seferian, Andrei; Jevnikar, Mitja; Roche, Anne; Bulifon, Sophie; Bourdin, Arnaud; Chaouat, Ari; Cottin, Vincent; Bertoletti, Laurent; Savale, Laurent; Humbert, Marc; Sitbon, Olivier; Montani, David

Evidentiary basis of the first regulatory qualification of a digital primary efficacy endpoint

数字主要疗效终点首次监管资格认定的证据基础

Servais, Laurent; Strijbos, Paul; Poleur, Margaux; Mirea, Andrada; Butoianu, Nina; Sansone, Valeria A; Vuillerot, Carole; Schara-Schmidt, Ulrike; Scoto, Mariacristina; Seferian, Andreea M; Previtali, Stefano C; Tulinius, Már; Nascimento, Andrés; Furlong, Pat; Singh, Teji; Dreghici, Roxana Donisa; Goemans, Nathalie; Mercuri, Eugenio; Straub, Volker; Ormazabal, Maitea Guridi; Braid, Jessica; Muntoni, Francesco; Tricot, Alexis; Annoussamy, Mélanie; Eggenspieler, Damien