日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Customizable virus-like particles deliver CRISPR-Cas9 ribonucleoprotein for effective ocular neovascular and Huntington's disease gene therapy.

可定制的病毒样颗粒递送 CRISPR-Cas9 核糖核蛋白,用于有效的眼部新生血管和亨廷顿病基因治疗

Ling Sikai, Zhang Xue, Dai Yao, Jiang Zhuofan, Zhou Xujiao, Lu Sicong, Qian Xiaoqing, Liu Jianping, Selfjord Niklas, Satir Tugce Munise, Lundin Anders, Touza Julia Liz, Firth Mike, Van Zuydam Natalie, Bilican Bilada, Akcakaya Pinar, Hong Jiaxu, Cai Yujia

Dual inhibition of DNA-PK and PolÏ´ boosts precision of diverse prime editing systems.

DNA-PK 和 PolÏ´ 的双重抑制提高了各种主要编辑系统的精确度

Dacquay Louis C, Antoniou Panagiotis, Mentani Astrid, Selfjord Niklas, MÃ¥rtensson Hanna, Hsieh Pei-Pei, Mustfa Salman, Thom George, Wimberger Sandra, Firth Mike, Akrap Nina, Maresca Marcello, Peterka Martin

Engineered PsCas9 enables therapeutic genome editing in mouse liver with lipid nanoparticles

利用脂质纳米颗粒对小鼠肝脏进行基因工程改造的PsCas9基因编辑,可实现治疗性基因组编辑。

Degtev, Dmitrii; Bravo, Jack; Emmanouilidi, Aikaterini; Zdravković, Aleksandar; Choong, Oi Kuan; Liz Touza, Julia; Selfjord, Niklas; Weisheit, Isabel; Francescatto, Margherita; Akcakaya, Pinar; Porritt, Michelle; Maresca, Marcello; Taylor, David; Sienski, Grzegorz