日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Preclinical efficacy and safety of AAVrh10-based plakophilin-2 gene therapy (LX2020) as a treatment for arrhythmogenic cardiomyopathy.

基于 AAVrh10 的 plakophilin-2 基因疗法 (LX2020) 治疗致心律失常性心肌病的临床前疗效和安全性

Zhang Jing, Gutierrez-Lara Erika Joana, Do Aryanne, Nguyen Lena, Nair Anju, Selvan Nithya, Fenn Tim, Adler Eric, Khanna Richie, Sheikh Farah

Validation of Anti-Adeno Associated Virus Serotype rh10 (AAVrh.10) Total and Neutralizing Antibody Immunogenicity Assays

抗腺相关病毒rh10血清型(AAVrh.10)总抗体和中和抗体免疫原性检测的验证

Butala-Flores, Elizabeth; Nguyen, Thien; Selvan, Nithya; Armstrong, Luke; Miller, Michelle; Kamen, Lynn; Lester, Todd; Wernyj, Roman; Khanna, Richie; McNally, Jim; Hays, Amanda

Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease

在非人灵长类动物中,通过脑池内给药评估 AAVrh.10hCLN2 治疗 CLN2 巴顿病的安全性和生物分布

De, Bishnu P; Rosenberg, Jonathan B; Selvan, Nithya; Wilson, Isabelle; Yusufzai, Nadir; Greco, Alessandria; Kaminsky, Stephen M; Heier, Linda A; Ricart Arbona, Rodolfo J; Miranda, Ileana C; Monette, Sebastien; Nair, Anju; Khanna, Richie; Crystal, Ronald G; Sondhi, Dolan

O-GlcNAcase Fragment Discovery with Fluorescence Polarimetry

利用荧光偏振法发现 O-GlcNAcase 片段

Borodkin, Vladimir S; Rafie, Karim; Selvan, Nithya; Aristotelous, Tonia; Navratilova, Iva; Ferenbach, Andrew T; van Aalten, Daan M F