日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Engineered hematopoietic stem cells give rise to therapeutic antibody secreting B cells

经基因工程改造的造血干细胞可产生分泌治疗性抗体的B细胞。

Porteus, Matthew; Luna, Sofia; Feist, William; Utz, Ashley; Afaghani, Jumana; Miyauchi, Masashi; Ghanim, Hana; Ekman, Freja; Amaya, Anais; Selvaraj, Sridhar; Russkamp, Norman; Schmiderer, Ludwig

Harnessing DNA barcoding to enhance and sustain polyclonality in gene-edited hematopoietic stem cells.

利用DNA条形码增强和维持基因编辑造血干细胞的多克隆性。

Ojeda-Perez Isabel, Bustos Andrés, Selvaraj Sridhar, Fañanas-Baquero Sara, Alberquilla-Fernandez Omaira, Serrano Luis-Javier, Bonafont Jose, Garcia-Torralba Aida, Torres-Ruiz Raul, Rodriguez-Perales Sandra, Lang Valeri, Trigueros Cesar, Mayo-Garcia Rafael, Quintana-Bustamante Oscar, Porteus Matthew, Sánchez-Dominguez Rebeca, Segovia Jose-Carlos

Enhancement of erythropoietic output by Cas9-mediated insertion of a natural variant in haematopoietic stem and progenitor cells.

通过 Cas9 介导将天然变异体插入造血干细胞和祖细胞,增强红细胞生成输出

Luna Sofia E, Camarena Joab, Hampton Jessica P, Majeti Kiran R, Charlesworth Carsten T, Soupene Eric, Selvaraj Sridhar, Jia Kun, Sheehan Vivien A, Cromer M Kyle, Porteus Matthew H

Transplantation studies reveal internuclear transfer of toxic RNA in engrafted muscles of myotonic dystrophy 1 mice

移植研究揭示了强直性肌营养不良1型小鼠移植肌肉中毒性RNA的核间转移。

Mondragon-Gonzalez, Ricardo; Azzag, Karim; Selvaraj, Sridhar; Yamamoto, Ami; Perlingeiro, Rita C R