日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CFAP20 salvages arrested RNAPII from the path of co-directional replisomes

CFAP20 可阻止 RNAPII 进入同向复制体的路径

Uruci, Sidrit; Boer, Daphne E C; Chrystal, Paul W; Lalonde, Maxime; Panagopoulos, Andreas; Yakoub, George; Kirdök, Idil; de Lint, Klaas; van der Woude, Melanie; Wendel, Tiemen J; Brussee, Sem J; Wondergem, Annelotte P; van Overbeek, Nila K; Schotman, Nini; Lingeman, Jolanthe; Ljungman, Mats; van Oudenaarden, Alexander; van Attikum, Haico; Vertegaal, Alfred C O; Noordermeer, Sylvie M; Wolthuis, Rob M F; Altmeyer, Matthias; Hamperl, Stephan; Tropepe, Vincent; van den Berg, Jeroen; van den Heuvel, Diana; Luijsterburg, Martijn S

Global determinants of coastal migration under climate change

气候变化背景下沿海人口迁移的全球决定因素

Duijndam, Sem J; Botzen, W J Wouter; Hagedoorn, Liselotte C; Ton, Marijn; de Bruijn, Jens; Carretero, Silvina; Dachary-Bernard, Jeanne; Rulleau, Bénédicte; Aerts, Jeroen C J H

Calcium binding by γ-carboxyglutamic acid: it takes two to tether

γ-羧基谷氨酸与钙的结合:需要两个分子才能连接

Ippel, Hans; Peijnenborgh, Sem J; Hackeng, Tilman M; Agten, Stijn M

Anticipating sea-level rise and human migration: A review of empirical evidence and avenues for future research

预测海平面上升和人口迁移:实证证据回顾及未来研究方向

Duijndam, Sem J; Botzen, Wouter J W; Hagedoorn, Liselotte C; Aerts, Jeroen C J H

A Quantitative In Vitro Potency Assay for Adeno-Associated Virus Vectors Encoding for the UGT1A1 Transgene

编码 UGT1A1 转基因的腺相关病毒载体的体外定量效力测定

Sem J Aronson, Robert S Bakker, Sascha Moenis, Remco van Dijk, Giulia Bortolussi, Fanny Collaud, Xiaoxia Shi, Suzanne Duijst, Lysbeth Ten Bloemendaal, Giuseppe Ronzitti, Andrés F Muro, Federico Mingozzi, Ulrich Beuers, Piter J Bosma

Efficacy of AAV8-h UGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients

AAV8-h UGT1A1 与雷帕霉素对新生大鼠、哺乳大鼠和幼年大鼠的疗效,可作为儿童 CNs 患者治疗的模型

Xiaoxia Shi, Sem J Aronson, Lysbeth Ten Bloemendaal, Suzanne Duijst, Robert S Bakker, Dirk R de Waart, Giulia Bortolussi, Fanny Collaud, Ronald P Oude Elferink, Andrés F Muro, Federico Mingozzi, Giuseppe Ronzitti, Piter J Bosma

Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome

在克里格勒-纳贾尔综合征基因治疗背景下预先存在的抗腺相关病毒免疫的流行率和相关性

Sem J Aronson, Philippe Veron, Fanny Collaud, Aurélie Hubert, Virginie Delahais, Géraldine Honnet, Robert J de Knegt, Norman Junge, Ulrich Baumann, Angelo Di Giorgio, Lorenzo D'Antiga, Virginia M Ginocchio, Nicola Brunetti-Pierri, Philippe Labrune, Ulrich Beuers, Piter J Bosma, Federico Mingozzi

Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome

用于治疗 Crigler-Najjar 综合征的 AAV8-hUGT1A1 载体的临床前开发

Fanny Collaud, Giulia Bortolussi, Laurence Guianvarc'h, Sem J Aronson, Thierry Bordet, Philippe Veron, Severine Charles, Patrice Vidal, Marcelo Simon Sola, Stephanie Rundwasser, Delphine G Dufour, Florence Lacoste, Cyril Luc, Laetitia V Wittenberghe, Samia Martin, Christine Le Bec, Piter J Bosma, An

Biliverdin Reductase inhibitors did not improve severe unconjugated hyperbilirubinemia in vivo

胆绿素还原酶抑制剂在体内并未改善严重的非结合型高胆红素血症。

van Dijk, Remco; Aronson, Sem J; de Waart, Dirk R; van de Graaf, Stan F; Duijst, Suzanne; Seppen, Jurgen; Elferink, Ronald Oude; Beuers, Ulrich; Bosma, Piter J

Emergence of hepatitis C virus genotype 4: phylogenetic analysis reveals three distinct epidemiological profiles

丙型肝炎病毒4型基因型的出现:系统发育分析揭示了三种不同的流行病学特征

de Bruijne, Joep; Schinkel, Janke; Prins, Maria; Koekkoek, Sylvie M; Aronson, Sem J; van Ballegooijen, Marijn W; Reesink, Hendrik W; Molenkamp, Richard; van de Laar, Thijs J W