日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Psychometric Properties and Meaningful Change Thresholds of the Vitiligo Area Scoring Index.

白癜风面积评分指数的心理测量特性和有意义的变化阈值

Ezzedine Khaled, Soliman Ahmed M, Camp Heidi S, Ladd Mary Kate, Pokrzywinski Robin, Coyne Karin S, Sen Rohini, Schlosser Bethanee J, Bae Jung Min, Hamzavi Iltefat

The Lived Experience of Patients Diagnosed with Vitiligo and a Preliminary Conceptual Disease Model: Insights from Patients, Patient Advocates, and Clinicians

白癜风患者的亲身经历及初步概念疾病模型:来自患者、患者权益倡导者和临床医生的见解

Ezzedine, Khaled; Soliman, Ahmed M; Ladd, Mary Kathleen; Patterson, Stavonnie; Sen, Rohini; Ofori, Sarah; Coyne, Karin S; Pokrzywinski, Robin

Update and European consensus on a patient-centered core outcome set for multiple myeloma in clinical practice and research

关于多发性骨髓瘤临床实践和研究中以患者为中心的核心结局指标集的更新和欧洲共识

Oerlemans, Simone; De Rooij, Belle H; Bennink, Christine; Bullinger, Lars; Broijl, Annemiek; D'Agostino, Mattia; Laane, Edward; Lupo-Stanghellini, Maria Teresa; Perrot, Aurore; Wester, Ruth; Cursaru, Viorica; Scheurer, Hans; Vesseur, Jan; Dalal, Mehul; Sen, Rohini; Stamm, Tanja; Ludwig, Heinz; Sonneveld, Pieter

Psychometric Analysis of the Patient-Reported Hypoparathyroidism Symptom Diary Symptom Subscale Using Data from Two Clinical Trials

利用两项临床试验的数据对患者自述甲状旁腺功能减退症状日记症状分量表进行心理测量分析

Nelson, Lauren; Ing, Steven W; Rubin, Mishaela R; Ma, Jia; Martin, Susan; Sen, Rohini; Ayodele, Olulade

S131: REGIONAL ASSESSMENT OF THE EXPERIENCES OF HEALTHCARE PROFESSIONALS (HCPS) TREATING PATIENTS WITH SICKLE CELL DISEASE (SCD): THE INTERNATIONAL SICKLE CELL WORLD ASSESSMENT SURVEY (SWAY)

S131:对治疗镰状细胞病 (SCD) 患者的医护人员 (HCPS) 经验的区域评估:国际镰状细胞世界评估调查 (SWAY)

Hibbs, Stephen; Weisel, Katja; Hungria, Vania; Quach, Hang; Yoon, Sung-Soo; Rodríguez-Otero, Paula; Kroog, Glenn; Sinha, Arijit; Boyapati, Anita; Lyon, Charlotte; Lorenc, Karen Rodriguez; Inocencio, Timothy; Harnett, James; Chi, Lei; Moore, Vygngley; Voorhees, Peter; Toreli, Ana Carolina; Campos, Paula De Melo; Toni, Isabella; Leonardo, Daniela Pinheiro; Lanaro, Carolina; de Albuquerque, Dulcineia Martins; Fertrin, Kleber Yotsumoto; Costa, Fernando F; Amato, Viviana; Fusani, Stefania; Papayannidis, Cristina; Nanni, Jacopo; Curti, Antonio; Marchesi, Francesco; Fanciulli, Maurizio; Simonetti, Giorgia; Musuraca, Gerardo; Marconi, Giovanni; Gottardi, Michele; Sperotto, Alessandra; Rossi, Alessandra; Maraglino, Alessio Maria Edoardo; Sammassimo, Simona; Gigli, Federica; Todisco, Elisabetta; Tarella, Corrado; Giglio, Fabio; Derenzini, Enrico; Dierickx, Daan; Connerotte, Thierry; Dallemagne, Julie; Becker, Ann De; Moors, Ine; Snauwaert, Sylvia; Sonet, Anne; Theunissen, Koen; Breems, Dimitri; Prijck, Bernard De; Jaspers, Aurélie; Lambert, Catherine; Heyrman, Bert; Hautekiet, Joris; Lyna, Sofie; Maertens, Chantal; Delrieu, Vanessa; Hultcrantz, Malin; Kleinman, David; Vij, Ravi; Escalante, Fernando; Delforge, Michel; Kotowsky, Nirali; Bitetti, Jacopo; Boytsov, Natalie; Camadoo-O’byrne, Leena; Happ, Lindsey Powers; Rohman, Mujib; Germain, Guillaume; Duh, Mei Sheng; Laliberté, François; Mahendran, Malena; Urosevic, Ana; Lee, Hans C; Martini, Gianluca; Zappasodi, Patrizia; Ferretti, Virginia Valeria; Calabretta, Ludovica; Gelli, Eleonora; Cabrera, Claudia Patricia Tobar; Rossi, Marianna; Roncoroni, Elisa; Arcaini, Luca; Zeidan, Amer M; Butrym, Aleksandra; Yucel, Aylin; Deshpande, Gaurav; Che, Min; Gu, Tao; Xiao, Hong; Miteva, Dimana; Nadal, Jose Alberto; Le, T Kim; Symeonidis, Argiris; Yu, Dan; Cheng, Hui; Guo, Jingming; Jiang, Rui; Zhang, Youshan; Wan, Chucheng; Qin, Jun; Yuan, Guolin; Chen, Shiming; Yang, Zhuangzhi; Hu, Junbin; Zhang, Yicheng; LI, Weiming; Butt, Ayesha; Garcia-Milian, Rolando; Goshua, George; Gu, Sean; Hwa, John; Chun, Hyung; Belmont, H Michael; Kello, Nina; Branch, D Ware; Petri, Michelle; Knight, Jason S; Willis, Rohan; Bertolaccini, Maria Laura; Erkan, Doruk; Lee, Alfred; Sharda, Anish; Pine, Alexander; Shah, Nirmish; Brown, Clark; Andemariam, Biree; Idowu, Modupe; Glaros, Alexander; Cronin, Robert M; Moehring, Barbara; Hoppe, Carolyn; Dixon, Sandy; Hayward, Brooke; Purdie, David M; Meier, Emily Reihm; Manwani, Deepa; Fu, Haixia; An, Zhuo-Yu; Huang, Qiu-Sha; Wu, Ye-Jun; Meng, Feitong; Wang, Song; Feng, Chengjie; Tong, Keting; Jing, Yue; LI, Yimeng; LI, Xueqi; LI, Menglin; Xiao, Mengyu; Chen, Yuxiu; Zhao, Chen; Zhou, Jianying; Zhang, Xiao-Hui; Huang, Xiao-Jun; Siala, Nour; Derbel, Yousra Fakhfakh; Amor, Imen Ben; Chaari, Mourad; Kassar, Olfa; Jdidi, Ines; Frikha, Imen; Louati, Nour; Kallel, Faten; Charfi, Maha; Sannena, Hlima; Mnif, Samia; Latifa, Khelifa; Mallek, Rahma; Mseddi, Sondes Hadiji; Medhaffar, Moez; Saad, Ali; Amor, Ikram Ben; Kallel, Choumous; Elloumi, Moez; Sannipoli, Daniele; Camilla, Gariazzo; Farina, Francesca; Diral, Elisa; Bruno, Alessandro; Clerici, Daniela; Marktel, Sarah; Canziani, Luca; Catalano, Gloria; Fiore, Paolo; Oltolini, Chiara; Querini, Patrizia Rovere; Corti, Consuelo; Ciceri, Fabio; Vitali, Giordano; Lupo-Stanghellini, Maria Teresa; van Beers, Eduard; Al-Samkari, Hanny; Grace, Rachael F; Barcellini, Wilma; Glenthøj, Andreas; Beynon, Vanessa; Wind-Rotolo, Megan; Xu, Rengyi; Dibacco, Melissa; Patel, Parija; Porter, John B; Kuo, Kevin HM; Tam, Constantine; Shadman, Mazyar; Sharman, Jeff; Cull, Gavin; Phillips, Tycel; Trotman, Judith; Cohen, Aileen; Allewelt, Heather; Crescenzo, Rocco; Delarue, Richard; Zhang, Heather; Tariq, Bilal; Sahasranaman, Sri; Ou, Ying C; Flinn, Ian W; Jang, Jun Ho; Kim, Jin Seok; Lim, Cindy Thiow Koon; Kleinman, Nora J; Myren, Karl-Johan; Wang, Alice; Patel, Yogesh; Lee, Jong Wook; Chang, Soon Hee; Ham, Ji Yeon; Kim, Yu Kyung; Suh, Jang Soo; Kumode, Takahiro; Munakata, Wataru; Goto, Hideki; Fukuhara, Noriko; Shimoyama, Tatsu; Takeuchi, Masahiro; Kawakita, Toshiro; Kubo, Kohmei; Sawa, Masashi; Uchida, Toshiki; Mishima, Yuko; Ichii, Michiko; Hanaya, Miyoko; Matsumoto, Asuka; Kuriki, Masaaki; Izutsu, Koji; Ishizawa, Kenichi; Mehta-Shah, Neha; Jacobsen, Eric; Luigi Zinzani, Pier; Zain, Jasmine; Mead, Monica; Casulo, Carla; Gritti, Giuseppi; Pinter-Brown, Lauren; Izutsu, Koji; Waters, Sheila; Brammer, Jonathan; Pro, Barbara; Horwitz, Steven; Oh, Danielle H; MA, Xiao; He, Jackson; Kearney, Conor; Hogg, Simon J; Newbold, Andrea; Fraser, Peter; Jennings, Ian G; Brasacchio, Daniella; Susanto, Olivia; Yew Fong, Chun; Dawson, Mark A; Gruber, Emily; Kats, Lev; Johnstone, Ricky W; Thompson, Philip E; Shortt, Jake; Cai, Qingqing; LI, Chaofeng; Wang, Liang; Xie, Chuanmiao; Zhang, Yuchen; Deng, Yishu; Zou, Qihua; Jing, Bingzhong; Cai, Peiqiang; Tian, Xiaopeng; Cao, Yi; Yang, Yu; LI, Bingzong; Liu, Fang; LI, Zhihua; Liu, Zaiyi; Feng, Shiting; Peng, Tingsheng; Dong, Yujun; Wang, Xinyan; Ruan, Guangying; He, Yun; Huang, Huiqiang; Liang, Yang; Zhang, Huilai; Cheng, Ying; Yang, Hai-Yan; Zhang, Liling; Zou, Liqun; Guo, Ye; Cao, Junning; Huang, Huiqiang; Wang, Zhao; Huang, Sha; Liang, Zhiyu; Lyu, Jiaoyan; Fang, Yiqian; Cohen, Aileen; Zhou, Keshu; Diepers, Alice; Schulze, Susann; Jäkel, Nadja; Misiak, Danny; Zahn, Christina; Spohn, Claudia; Moeller, Regina; Kämpfe, Dietrich; Schwarz, Maik; Nerger, Katrin; Edemir, Bayram; Kathrin Al-Ali, Haifa; Ho Yi, Jun; Park, Sung-Soo; Min, Chang-Ki; Eom, Hyeon-Seok; Koh, Youngil; Min Byun, Ja; Yoon, Sung-Soo; Hoon Lee, Jae; Jung, Sung-Hoon; Lee, Je-Jung; Eun Yoon, Sang; Kim, Kihyun; Wang, Rong; Shen, Wenyi; Shi, Zhongxun; Zhang, Yuan; Wei, Liangmin; Duan, Minghui; Xiao, Min; Wang, Jin; Chen, Suning; Wang, Qian; Huang, Jianyao; Hu, Xiaomei; Mei, Jinhong; List, Yang; Chen, Feng; LI, Jianyong; Wei, Yongyue; Harrison, Claire; Mascarenhas, John; Cilloni, Daniela; Schlenk, Richard; Jacoby, Brian; Slack, Robert J; Aslanis, Vassilios; Singh, Bhupinder; Lindmark, Bertil; Verstovsek, Srdan; Rampal, Raajit K; Abonour, Rafat; Rifkin, Robert; Ailawadhi, Sikander; Lee, Hans C; Gasparetto, Christina; Wagner, Lynne; Durie, Brian; Hardin, James; Terebelo, Howard; Narang, Mohit; Toomey, Kathleen; Tang, Yuexin; Dhanasiri, Sujith; Anand, Jasmeet; Yu, Edward; Marshall, Thomas; Liu, Liang; Jagannath, Sundar; Bielowski, Anna; Kilian, Teresa; Vera-Cruz, Sarah Rümpeler Calheiros; Riester, Zeno; Prommersberger, Sabrina; Beckmann, Julia; Kortüm, Martin; Rasche, Leo; Einsele, Hermann; Hudecek, Michael; Danhof, Sophia; Iyer, Swaminathan; Jagadeesh, Deepa; Domingo Domènech, Eva; Benedetti, Fabio; Rodriguez Izquierdo, Antonia; Bouabdallah, Kamal; Vitolo, Umberto; Illidge, Tim; Liu, Jingmin; Knowles, Scott; Horwitz, Steven; Franke, Georg-Nikolaus; Ussmann, Jule; Backhaus, Donata; Henrik Nicolay, Nils; Vucinic, Vladan; Herling, Marco; Schetschorke, Birthe; Hell, Saskia; Platzbecker, Uwe; Schwind, Sebastian; Jentzsch, Madlen; Tucci, Francesca; Consiglieri, Giulia; Filisetti, Chiara; De Pellegrin, Maurizio; Mellone, Renata; Fumagalli, Francesca; Darin, Silvia; Sarzana, Marina; Scarparo, Stefano; Ciotti, Francesca; Silvani, Paolo; Baldoli, Cristina; Pontesilli, Silvia; Parini, Rossella; la Marca, Giancarlo; Ciceri, Fabio; Naldini, Luigi; Aiuti, Alessandro; Gentner, Bernhard; Ester Bernardo, Maria; Jeyaraju, Danny; Hayati, Sheida; Polonskaia, Ann; Browne, Andrew; Risueño, Alberto; Hagner, Patrick; Gupta, Vikas; Talpaz, Moshe; Hernandez, Christopher; Chia, Vincent; Brown, Patrick; De Menezes, Daniel Lopes; La Motte-Mohs, Ross; Nvs Suragani, Rajasekhar; Gandhi, Anita; Lakhwani, Sunil Lakhwani; Santana, Ignacio Artiles; Pérez-Pinilla, Belén; Garcia, Alvaro Bienert; Saavedra, Minerva Montalvo; Díaz-Lopez, Marta; De Bonis-Braun, Carolina; Salazar, María José Rodríguez; Machado-Machado, Patricia; Garcia, Miguel Teodoro Hernandez; Raya, Jose Maria; Kenet, Gili; Nolan, Beatrice; Zulfikar, Bulent; Antmen, Bulent; Kampmann, Peter; Matsushita, Tadashi; You, Chur-Woo; Vilchevska, Kateryna; Bag, Catherine N; Sharif, Azizan; Peyvandi, Flora; Young, Guy; Negrier, Claude; Sussebach, Christian; Shammas, Fadi; Andersson, Shauna; Mei, Baisong; Kavakli, Kaan; Escherich, Carolin; Chen, Wenan; Yang, Wenjian; Teachey, David T; Raetz, Elizabeth A; Devidas, Meenakshi; Wu, Gang; Nichols, Kim E; Inaba, Hiroto; Pui, Ching-Hon; Jeha, Sima; Hunger, Stephen P; Loh, Mignon L; Yang, Jun J; Rubnitz, Jeffrey; C. Issa, Ghayas; M. Stein, Eytan; Shukla, Neerav; Stock, Wendy; Žučenka, Andrius; Khazal, Sajad; Khera, Nandita; Stieglitz, Elliot; Rubinstein, Jeremy; Rosen, Galit; Ghiraldi, Rachel; Van Nguyen, Huy; Mcneer, Nicole; Zwaan, C Michel; Lang, Fabian; Pfeifer, Heike; Raffel, Simon; Fiedler, Walter; Hanoun, Maher; Hänel, Mathias; Spriewald, Bernd; Viardot, Andreas; Vucinic, Vladan; Serve, Hubert; Hoelzer, Dieter; Gökbuget, Nicola; Boer, Judith M; Ilan, Uri; Hoen, Babette DJ; Boeree, Aurelie; Langenberg, Karin PS; Koster, Jan; Bourquin, Jean-Pierre; Molenaar, Jan J; Goemans, Bianca; den Boer, Monique L; Zwaan, Michel; Carpenedo, Monica; Broome, Catherine M; Mcdonald, Vickie; Miyakawa, Yoshitaka; Kuter, David; Al-Samkari, Hanny; Bussel, James; Matthijssens, Filip; Hultberg, Anna; Ayguasanosa Dachs, Jaume; De Beuf, Kristof; Rodeghiero, Francesco; Michel, Marc; Newland, Adrian; Holstein, Sarah A; Mian, Hira; Touzeau, Cyrille; Kingsley, Edwin; Vogl, Dan; Zuniga, Richard; Suryanarayan, Kaveri; Wang, Shining; Thesillat-Versmee, Laura; Liu, Yuyin; Chen, Tian; Zhang, Yefei; Parot, Xavier; Lee, Hans C; Pereira-Martins, Diego A; Alexander Ortiz Rojas, César; Weinhauser, Isabel; Silveira, Douglas; Wierenga, Albertus T J; van den Boom, Vincent; Bianco, Thiago M; Ammatuna, Emanuele; Quek, Lynn; Lucena-Araujo, Antonio R; Huls, Gerwin; Rego, Eduardo; Jacob Schuringa, Jan; Rossi, Marica; Diallo, Dapa; Tolo, Aissata; Diop, Saliou; Diagne, Ibrahima; Belinga, Suzanne; Kitenge, Robert; Kouakou, Boidy; Kamara, Ismael; Traore, Youssouf; Ly, Indou Deme; Diaw, Mor; Tshilolo, Leon; Ranque, Brigitte; Piras, Giovanna; Cucca, Antonella; Monne, Maria Itria; Uras, Antonella; Longu, Francesco; Calvisi, Anna; Isoni, Maria Antonia; Cambosu, Francesca; Campus, Paola Maria; Murineddu, Marco; Arru, Luigi Benedetto; Bianchi, Alessandro; Murgia, Alessandro; Vacca, Melissa; Fozza, Claudio; Palmas, Angelo Domenico; van Dijk, Myrthe; Rab, Minke; van Oirschot, Brigitte; Bos, Jennifer; Derichs, Cleo; Rijneveld, Anita; Cnossen, Marjon; Nur, Erfan; Biemond, Bart; Bartels, Marije; Jans, Judith; van Solinge, Wouter; Schutgens, Roger; Van Wijk, Richard; van Beers, Eduard; Duminuco, Andrea; Nardo, Antonella; Orofino, Alessandra; Romano, Alessandra; Figuera, Amalia Stefania; Chiarenza, Annalisa; Markovic, Uros; Caruso, Laura; Giunta, Giuliana; Leotta, Salvatore; Milone, Giuseppe; Cupri, Alessandra; Conticello, Concetta; Fabro, Vittorio Del; Mauro, Elisa; Maugeri, Cinzia; Vetro, Calogero; Parisi, Marina; Raimondo, Francesco DI; Palumbo, Giuseppe; Ciceri, Fabio; Peffault de Latour, Régis; Devillier, Raynier; Chiusolo, Patrizia; Bauquet, Aurelie; Simons, Laura; Heimendinger, Pierre; Gaudeaux, Pierre; Negre, Olivier; Soheili, Tayebeh-Shabi; Paillet, Juliette; Andre, Isabelle; Oster, Sebastien; Cavazzana, Marina; Lehmann, Frederic; Zhu, Xiaolu; Jiang, Qian; Lu, Jin; Sun, Yuqian; Zhao, Xiaosu; Yang, Shenmiao; Tang, Feifeis; Yu, Wenjing; Zhao, Ting; Liu, Xiaohong; Jia, Jinsong; Duan, Wenbing; Hu, Lijuan; Wang, Jing; Liu, Yang; Peng, Nan; Dou, Xuelin; MA, Rui; Fu, Qiang; Wang, Huifang; Liu, Kaiyan; Huang, Xiaojun; Jiang, Hao; Martinez-Verbo, Laura; Villanueva, Lorea; Llinàs-Arias, Pere; Antonio García-Prieto, Carlos; Piñeyro, David; Oliver-Caldes, Aina; García-Ortiz, Almudena; Valeri, Antonio; De Larrea, Carlos Fernández; Martínez-López, Joaquin; Ferrer, Gerardo; Esteller, Manel; Geva, Mika; Fried, Shalev; Itzhaki, Orit; Shem-Tov, Noga; Danylesko, Ivetta; Yerushalmi, Ronit; Marcus, Ronit; Sdayoor, Inbal; Shapira-Frommer, Ronnie; Kedmi, Meirav; Shouval, Roni; Nagler, Arnon; Shimoni, Avichai; Avigdor, Abraham; Albinger, Nawid; Bexte, Tobias; Al-Ajami, Ahmad; Wendel, Philipp; Buchinger, Leon; Gessner, Alec; Alzubi, Jamal; Särchen, Vinzenz; Vogler, Meike; Bhayadia, Raj; Klusmann, Jan-Henning; Möker, Nina; Cathomen, Toni; Rieger, Michael A; Imkeller, Katharina; Ullrich, Evelyn; Farina, Francesca; Sannipoli, Daniele; Oltolini, Chiara; Diral, Elisa; Marcatti, Magda; Ferla, Valeria; Canziani, Luca; Xue, Elisabetta; Greco, Raffaella; Clerici, Daniela; Bruno, Alessandro; Marktel, Sarah; Mastaglio, Sara; Carrabba, Matteo; Bernardi, Massimo; Carmagnola, Anna; Castagna, Antonella; Scarpellini, Paolo; Dell’acqua, Raffaele; Ciceri, Fabio; Peccatori, Jacopo; Corti, Consuelo; Lupo Stanghellini, Maria Teresa; Ghia, Paolo; Allan, John; Siddiqi, Tanya; Wierda, William G; Tam, Constantine; Moreno, Carol; Tedeschi, Alessandra; Szafer-Glusman, Edith; Zhou, Cathy; Abbazio, Chris; Dean, Jim; Szoke, Anita; Barr, Paul M; de Botton, Stéphane; Cluzeau, Thomas; Vigil, Carlos; Cook, Rachel; Rousselot, Philippe; Rizzieri, David; Liesveld, Jane; Fenaux, Pierre; Braun, Thorsten; Pigneux, Arnaud; Peterlin, Pierre; Paul, Sofia; Rajagopal, Nisha; Carulli, John; Roth, David; Volkert, Angela; Malak, Tanya Abdul; Kelly, Michael; Klimek, Virginia; Stein, Eytan; Berton, Guillaume; Vicier, Cécile; Hospital, Marie-Anne; Saillard, Colombe; Hicheri, Yosr; Maisano, Valerio; Villetard, Ferdinand; Rouzaud, Camille; Corda, Evelyne D’incan; Rey, Jerome; Mohty, Bilal; Charbonnier, Aude; Proux, Aurelien; Vey, Norbert; Goncalves, Anthony; Garciaz, Sylvain; Cooper, Nichola; Kruse, Caroline; Ghanima, Waleed; Provan, Drew; Tomiyama, Yoshiaka; Hou, Ming; Arnold, Donald; Santoro, Cristina; Zaja, Francesco; Lovrencic, Barbara; Morgan, Mervyn; Lahav, Leron; Winograd, Michal; Bailey, Tom; Haenig, Jens; Georget, Mahnouch; Bussel, James; Fattizzo, Bruno; Vercellati, Cristina; Marcello, Anna; Patel, Parija; Wind-Rotolo, Megan; Pettine, Loredana; Leoni, Simona; Fermo, Elisa; Bianchi, Paola; Zaninoni, Anna; Barcellini, Wilma; Pezzullo, Luca; Giudice, Valentina; D’addona, Matteo; Buonanno, Maria Teresa; Novellis, Danilo DE; Ferrara, Idalucia; Fontana, Raffaele; Guariglia, Roberto; Luponio, Serena; Martorelli, Maria Carmela; Mettivier, Laura; Serio, Bianca; Selleri, Carmine; Palandri, Francesca; Gröpper, Stefanie; Loschi, Michael; Bellesso, Marcelo; Grosicki, Sebastian; Giraldo, Pilar; Harrison, Claire; Clevenger, Tracy; Stuart, Nikki; Qamoos, Hope; Vosganian, Gregory; Rothbaum, Wayne P; Verstovsek, Srdan; Vachhani, Pankit; Lee, Myung-Won; Koh, Jeong Suk; Kang, Sora; Ryu, Hyewon; Song, Ik-Chan; Lee, Hyo-Jin; Yun, Hwan-Jung; Kim, Seon Young; Kim, Seong Soo; Jo, Deog-Yeon; Yuan, Linyu; Xiaohui, Suo; Bai, Guanchen; LI, Hong; Han, Zhongjing; Zhang, Congcong; LI, Yinling; Gao, Sifeng; Zhang, Jilei; Lu, Xinxiao; Liu, Kaiqi; Xingli, Zhao; Le Coutre, Philipp; Göthert, Joachim; Saussele, Susanne; Pelzer, Uwe; Bullinger, Lars; Elmaagacli, Ahmet; Jehn, Christian; Stegelmann, Frank; Hochhaus, Andreas; Ernst, Thomas; Burchert, Andreas; Barcellini, Wilma; Michel, Marc; Cuker, Adam; Cooper, Nichola; Ghanima, Waleed; Wong, Raymond; Zaja, Francesco; Zhang, Fengkui; Bezlyak, Vladimir; Nguyen, Thu Thuy; Al-Samkari, Hanny; Bazinet, Alexandre; Arani, Naszrin; Chien, Kelly; Hammond, Danielle; Kadia, Tapan; Borthakur, Gautam; Alvarado, Yesid; Sasaki, Koji; Dinardo, Courtney; Pemmaraju, Naveen; Masarova, Lucia; Short, Nicholas; Yilmaz, Musa; Daver, Naval; Jabbour, Elias; Ravandi, Farhad; Kanagal-Shamanna, Rashmi; Pierce, Sherry; Kantarjian, Hagop; Garcia-Manero, Guillermo; Montalban-Bravo, Guillermo; Aguirre, Luis E; Jain, Akriti; Ball, Somedeb; Al Ali, Najla; Sallman, David; Kuykendall, Andrew; Chan, Onyee; Xie, Zhuoer; Walker, Alison; Sweet, Kendra; Lancet, Jeffrey; Padron, Eric; S. Komrokji, Rami; Selwyn Stein, Anthony; Jongen-Lavrencic, Mojca; Garciaz, Sylvain; A Huls, Gerwin; Maiti, Abhishek; Boissel, Nicolas; De Botton, Stephane; Fleming, Shaun; Michel Zwaan, C; C. de Leeuw, David; Desai, Pinkal; Lucia Arellano, Martha; Avigan, David; Langemeijer, Saskia; Jensen, Kyle; Wagenaar, Timothy; MI, Gu; Abbadessa, Giovanni; Bajel, Ashish; Charalampopoulou, Stella; Chapiro, Elise; Nadeu, Ferran; Zenz, Thorsten; Beà, Silvia; Roos-Weil, Damien; Bernard, Olivier; Susin, Santos A; Matutes, Estella; Campo, Elias; Duran-Ferrer, Martí; Nguyen-Khac, Florence; Ignacio Martín-Subero, José; Franke, Georg-Nikolaus; Loewe, Gunnar; Reiser, Marcel; Linde, Hartmut; Josting, Andreas; von der Heyde, Eyck; Weide, Rudolf; Tesch, Hans; Nusch, Arndt; Dengler, Jolanta; Jentsch-Ullrich, Kathleen; Linton, Kim; Doorduijn, Jeanette; El-Sharkawi, Dima; Mous, Rogier; Forconi, Francesco; Lewis, David; Gleeson, Mary; Riches, John; Mckay, Pam; Stevens, Wendy; Injac, Sarah G; Collins, Graham P; Fleming, Shaun; Roboz, Gail; T. Fathi, Amir; Y. Zhang, Tian; Wei, Andrew; Carraway, Hetty; Holes, Leanne; Petrlik, Erica; Prebet, Thomas; Lopes De Menezes, Daniel; Bluemmert, Iryna; Sun, Hao; Ravandi, Farhad; Moore, Elizabeth; Harrison, Simon; Ho, P Joy; Irving, Adam; King, Tracy; Mccaughan, Georgia; Mcquilten, Zoe; Mollee, Peter; Park, Susanna; Petrie, Dennis; Reynolds, John; Rutherford, Claudia; van Tonder, Tina; Wellard, Cameron; Wood, Erica; Spencer, Andrew; Yilmaz, Hulya; Seval, Guldane Cengiz; Toprak, Selami Kocak; Yuksel, Meltem Kurt; Topcuoglu, Pervin; Arslan, Onder; Demirer, Taner; Kuzu, Isinsu; Beksac, Meral; Ozcan, Muhit; Chien, Kelly; Urrutia, Samuel; LI, Ziyi; Kanagal-Shamanna, Rashmi; Almanza, Emmanuel; Abuasab, Tareq; Gener, Georgina; Bataller, Alex; Bazinet, Alexandre; Montalban-Bravo, Guillermo; Short, Nicholas; Jabbour, Elias; Kadia, Tapan; Ravandi, Farhad; Borthakur, Gautam; Hammond, Danielle; Swaminathan, Mahesh; Sasaki, Koji; Pierce, Sherry; Kantarjian, Hagop; Garcia-Manero, Guillermo; Cho, Seok-Goo; Kim, Tae Min; Taszner, Michał; Chen, Tsai Yun; Chaudhry, Aafia; Ufkin, Melanie; Uppala, Amulya; Sabir, Ayesha; Mohamed, Hesham; Ambati, Srikanth; Bachy, Emmanuel; Gao, Yan; Zhang, Liling; Gao, Sujun; Yang, Yu; Zhang, Qing-Yuan; Zhang, Huilai; He, Pengcheng; LI, Fei; Jing, Hongmei; Grange, Susan; Bu, Lilian; Wang, Qianming; Wang, Yanjie; Huang, Huiqiang; Chantepie, Sylvain; Huguet, Françoise; Hunault, Mathilde; Roth Guepin, Gabrielle; Balsat, Marie; Pilar Gallego Hernanz, Maria; Joris, Magalie; Karangwa, Alexandre; Ojeda Uribe, Mario; Santagostino, Alberto; Maury, Sébastien; Kytölä, Sari; Vänttinen, Ida; Kuusanmäki, Heikki; Ruokoranta, Tanja; Kurkela, Mika; Kiiski, Johanna; Holopainen, Annasofia; Partanen, Anu; Kuusisto, Milla EL; Koskela, Sirpa; Räty, Riikka; Itälä-Remes, Maija; Ettala, Pia; Rimpiläinen, Johanna; Siitonen, Timo; Pyörälä, Marja; T. 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Cives, Mauro; Neri, Iria; Pacinella, Gaetano; Tuttolomondo, Antonino; Marano, Massimo; Muratore, Francesco; Broccoli, Alessandro; Zinzani, Pier Luigi; Didona, Biagio; Dagna, Lorenzo; Vaglio, Augusto; Cohen-Aubart, Fleur; Haddad, Fadi; Jabbour, Elias; Zoghbi, Marianne; Short, Nicholas; Senapati, Jayastu; Macaron, Walid; Nasnas, Cedric; Nasr, Lewis; Pemmaraju, Naveen; Jain, Nitin; Wierda, William G; Borthakur, Gautam; Montalban-Bravo, Guillermo; Ravandi, Farhad; Garcia-Manero, Guillermo; Kadia, Tapan; Chien, Kelly; Thankachan, Jennifer; Garris, Rebecca; Kantarjian, Hagop; Ghobadi, Armin; Aldoss, Ibrahim; Maude, Shannon; S Wayne, Alan; Bhojwani, Deepa; Bajel, Ashish; Dholaria, Bhagirathbhai; Faramand, Rawan; Mattison, Ryan; Rettig, Michael; Bakkacha, Ouiam; Muth, John; Pannunzio, Angela; Ramsey, Brett; Mcnulty, Eileen; Cooper, Matthew; Davidson-Moncada, Jan; Jacobs, Kenneth; Dipersio, John; Maio, Elena; Montanari, Mattia; Puglisi, Francesco; Nurra, Clara; Miglino, Maurizio; Colombo, Nicoletta; Carminati, Enrico; Zecchetti, Giada; Vernarecci, Chiara; Chies, Maria; Ferro, Beatrice; Zucchetti, Massimo; Cagnetta, Antonia; Cea, Michele; Tedone, Elisabetta; Massimo Lemoli, Roberto; Guolo, Fabio; Minetto, Paola; Yan, Nan; Zhou, Ya-Lan; Zhao, Ming-Yue; Liao, Ming-Yue; Wang, Chun-Yang; Wang, Xiao-Juan; Zhu, Jian-Hua; Jiang, Hao; Jiang, Qian; Chang, Ying-Jun; Xu, Lan-Ping; Zhang, Xiao-Hui; Huang, Xiao-Jun; Ruan, Guo-Rui; Frustaci, Anna Maria; Montillo, Marco; Rossi, Davide; Zinzani, Pier Luigi; Motta, Marina; Gaidano, Gianluca; Quaresmini, Giulia; Scarfò, Lydia; Pietrasanta, Daniela; Coscia, Marta; Deodato, Marina; Zamprogna, Giulia; Cairoli, Roberto; Stüssi, Georg; Zucca, Emanuele; Pileri, Stefano; Zenz, Thorsten; Tedeschi, Alessandra; Carpenedo, Monica; Poloni, Antonella; Morsia, Erika; Biondo, Mattia; Calvaruso, Giuseppina; Frison, Luca; Leuzzi, Livia; Merli, Anna; Paciullo, Francesco; Patriarca, Andrea; Zaja, Francesco; Carli, Giuseppe; Bruins, Wassilis; Duetz, Carolien; Groen, Kaz; Korst, Charlotte; de Jonge, Vera; Verkleij, Christie; Rentenaar, Rosa; Cosovic, Meliha; van de Donk, Niels WCJ; Zweegman, Sonja; Mutis, Tuna; Quaranta, Pamela; Basso-Ricci, Luca; Jofra Hernandez, Raisa; Maria Naldini, Matteo; Barcella, Matteo; Pacini, Guido; Pietrasanta, Carlo; Pugni, Lorenza; Pais, Giulia; Benedicenti, Fabrizio; Giannelli, Stefania; Monti, Ilaria; Darin, Silvia; Barera, Graziano; Tucci, Francesca; Ferrua, Francesca; Calbi, Valeria; Gentner, Bernhard; DI Micco, Raffaella; Montini, Eugenio; Calabria, Andrea; Merelli, Ivan; Mosca, Fabio; Ester Bernardo, Maria; Pia Cicalese, Maria; Aiuti, Alessandro; Serena, Scala; LI, Caixia; Wei, Jia; Peng, Liu; Huang, He; LI, Fei; Dong, Yujun; Cai, Qingqing; Yang, Shenmiao; Zhang, Xinyou; Zhou, Hui; Zhang, Lu; Shi, Zaixing; Liang, Zhiyu; Wu, Binghao; Zhou, Keshu; Wu, Depei; Lang, Fabian; Pemberton-Whiteley, Zack; Clements, Joannie; Ruiz, Cristina; Rea, Delphine; Machado, Lisa; Takahashi, Naoto; Moon, Sung-Ho; P Grigg, Andrew; Borowczak, Cornelia; Schuld, Peter; Frank, Pauline; Constantinescu, Cristina; Boquimpani, Carla; Cortes, Jorge; Piciocchi, Alfonso; Marconi, Giovanni; Cipriani, Marta; Messina, Monica; Guolo, Fabio; Minetto, Paola; Paoloni, Francesca; Cotugno, Francesca; DI Donato, Laura; Simonetti, Giorgia; Palmieri, Raffaele; Buccisano, Francesco; Fazi, Paola; Vignetti, Marco; M. Lemoni, Roberto; Venditti, Adriano; Martinelli, Giovanni; Girnius, Saulius K; Richter, Joshua; Lyons, Roger M; Bogard, Kimberly; Manda, Sudhir; Birhiray, Ruemu E; Yimer, Habte A; Tran, Kim; Kambhampati, Suman; Arora, Jyoti; Noga, Stephen; Rifkin, Robert; Sai Mittapalli, Amrutha; Katamesh, Bahga; Oum, Muhamad; He, Rong; Viswanatha, David; Greipp, Patricia; Nguyen, Phuong; Jevremovic, Dragan; Arana Yi, Cecilia; M Foran, James; Benga, Kebede; Gangat, Naseema; Mangaonkar, Abhishek; Saliba, Antoine; Patnaik, Mrinal; J Hogan, William; Litzow, Mark; Tefferi, Ayalew; Shah, Mithun; Alkhateeb, Hassan; Al-Kali, Aref; Hawkes, Eliza A; Kim, Tae Min; Namuduri, Manjusha; Risal, Ashish; Shen, Biyi; Flink, Dina; Zhu, Min; Nolan, Siobhán; Brouwer-Visser, Jurriaan; Chaudhry, Aafia; Ambati, Srikanth; Mohamed, Hesham; Cho, Seok-Goo; Offner, Fritz; Decaux, Olivier; Hulin, Cyrille; Anguille, Sébastien; Sophie Michallet, Anne; Costa, Luciano; Touzeau, Cyrille; Boyd, Kevin; Vishwamitra, Deeksha; Guo, Yue; Niu, Zhuolu; Larsen, Julie; Chen, Lingling; Banerjee, Arnob; Goldberg, Jenna; Matous, Jeffrey; Heger, Jan-Michel; Mattlener, Julia; Mammadova, Laman; Sobesky, Sophia; Cirillo, Melita; Altmüller, Janine; Kirst, Elisabeth; Reinke, Sarah; Klapper, Wolfram; Bröckelmann, Paul J; Ferdinandus, Justin; Ullrich, Roland T; Freihammer, Max; Awerkiew, Sabine; Lohmann, Mia; Klein, Florian; Nürnberg, Peter; Hallek, Michael; Engert, Andreas; Borchman, Peter; von Tresckow, Bastian; Borchmann, Sven; Chen, Xinfeng; Ping, Yu; LI, Ling; Zhang, Lei; Zhang, Xudong; Huang, Jianmin; Liu, Jia; LI, Gui; He, Jiaping; Zhang, Hua; Zhao, Wei; Weng, Lihong; Yin, Wenjie; Shen, Lianjun; Cao, Wei William; LI, Wenling; Zhang, Mingzhi; Zhang, Yi; Zaja, Francesco; Al-Samkari, Hanny; Michel, Marc; Ghanima, Waleed; Cooper, Nichola; Wong, Raymond; Barcellini, Wilma; Zhang, Fengkui; Marturano, Emerenziana; Peyrard, Severine; Cuker, Adam; Dussiau, Charles; Comont, Thibault; Knosp, Camille; Vergnolle, Ines; Bravetti, Clotilde; Canali, Alban; Houvert, Amandine; Largeaud, Laetitia; Daveaux, Christian; Zaroili, Laila; Friedrich, Chloe; Boussaid, Ismael; Zalmai, Loria; Almire, Carole; Beyne-Rauzy, Odile; Willems, Lise; Bouscary, Didier; Gandrillon, Olivier; Fontenay, Michaela; Kosmider, Oliver; Vergez, Francois; Chapuis, Nicolas; Gurney, Mark; Alkhateeb, Hassan; Shah, Syed; Bansal, Radhika; Hathcock, Matthew; Rosenthal, Allison; Kharfan-Dabaja, Mohamed; Kourelis, Taxiarchis; Patnaik, Mrinal; Chen, Dong; Al-Kali, Aref; Kenderian, Saad; Lin, Yi; Shah, Mithun; Gushiken, Lucas F S; Gotardo, Érica M F; Brito, Pâmela L; Linguet, Sarah L; Leonardo, Flávia C; Colin-Aronovicz, Yves; Kim, Caroline L V; Koehl, Bérengère; Costa, Fernando F; Conran, Nicola; Liu, Rongrong; Wang, LI; Xu, Hui; Yin, Xiaolin; Liang, Junbin; Xie, Wenqiang; Yang, Gaohui; LI, Yaoyun; Zhou, Yali; Shi, Lei; Xiao, Bin; Shi, Lingling; Shi, Zeyan; Zhou, Xuemei; Fang, Jianpei; Xu, Xiangmin; Lai, Yongrong; Huang, Junjiu; Zhang, Xinhua; Guolo, Fabio; Minetto, Paola; Pesce, Silvia; Ballerini, Filippo; Cea, Michele; Greppi, Marco; Bozzo, Matteo; Miglino, Maurizio; Tedone, Elisabetta; Bo, Alessandra; Serio, Alberto; Luchetti, Silvia; Candiani, Simona; Mora, Marco; Agostini, Vanessa; Nozza, Paolo; Del Zotto, Genny; Marcenaro, Emanuela; Lemoli, Roberto Massimo; Short, Nicholas; Macaron, Walid; Dinardo, Courtney; Daver, Naval; Yilmaz, Musa; Borthakur, Gautam; Montalban-Bravo, Guillermo; Garcia-Manero, Guillermo; Issa, Ghayas; Sasaki, Koji; Burger, Jan; Maiti, Abhishek; Alvarado, Yesid; Thankachan, Jennifer; Abramova, Regina; Nasr, Lewis; Nasnas, Cedric; Zoghbi, Marianne; Kadia, Tapan; Konopleva, Marina; Kantarjian, Hagop; Ravandi, Farhad; Gomez Rosas, Patricia; Marchetti, Marina; Giaccherini, Cinzia; Russo, Laura; Gamba, Sara; Verzeroli, Cristina; Julia Tartari, Carmen; Bolognini, Silvia; Schieppati, Francesca; Ticozzi, Chiara; Sarmiento, Roberta; Celio, Luigi; Masci, Giovanna; Tondini, Carlo; Petrelli, Fausto; Giuliani, Francesco; D’alessio, Andrea; De Braud, Filippo; Santoro, Armando; Labianca, Roberto; Gasparini, Giampietro; Falanga, Anna; Pratz, Keith; Lai, Catherine; Jonas, Brian A; Dinardo, Courtney; Bui, Cat N; Kamalakar, Rajesh; Potluri, Jalaja; Chang, Wei-Han; Sen, Rohini; Leblanc, Thomas W; Ernst, Thomas; Le Coutre, Philipp; Crysandt, Martina; Brümmendorf, Tim H; Franke, Georg-Nikolaus; Illmer, Thomas; Burchert, Andreas; Lang, Fabian; Saussele, Susanne; Lars Teichmann, Lino; Radsak, Markus; Krause, Stefan; Rinke, Jenny; Fabisch, Christian; Lang, Thomas; Pfirrmann, Markus; Hochhaus, Andreas; Luo, Yi; Gao, Lei; Liu, Jia; Yang, Luxin; Wang, Lu; Lai, Xiaoyu; Gao, Shichun; Liu, Lizhen; Zhao, Lu; Ye, Yishan; Wang, Manning; Liao, Shengyu; Shen, Lianju

Development and validation of Gaucher disease type 1 (GD1)-specific patient-reported outcome measures (PROMs) for clinical monitoring and for clinical trials

开发和验证戈谢病1型(GD1)特异性患者报告结局指标(PROMs),用于临床监测和临床试验

Elstein, Deborah; Belmatoug, Nadia; Deegan, Patrick; Göker-Alpan, Özlem; Hughes, Derralynn A; Schwartz, Ida Vanessa D; Weinreb, Neal; Bonner, Nicola; Panter, Charlotte; Fountain, Donna; Lenny, Andrew; Longworth, Louise; Miller, Rachael; Shah, Koonal; Schenk, Jörn; Sen, Rohini; Zimran, Ari

Results of a randomized double-blind study evaluating luvadaxistat in adults with Friedreich ataxia

一项评估luvadaxistat治疗成人弗里德赖希共济失调症的随机双盲研究结果

Wang, Hao; Norton, Jonathan; Xu, Lin; DeMartinis, Nicholas; Sen, Rohini; Shah, Ankit; Farmer, Jennifer; Lynch, David

Cancer stage knowledge and desire for information: mismatch in Latino cancer patients?

拉丁裔癌症患者的癌症分期知识与信息需求之间是否存在不匹配?

Costas-Muniz, Rosario; Sen, Rohini; Leng, Jennifer; Aragones, Abraham; Ramirez, Julia; Gany, Francesca