Five-Year Outcomes of Lenadogene Nolparvovec Gene Therapy in Leber Hereditary Optic Neuropathy
Lenadogene Nolparvovec基因疗法治疗Leber遗传性视神经病变的五年疗效
期刊:Jama Ophthalmology
影响因子:9.2
doi:10.1001/jamaophthalmol.2024.5375
Yu-Wai-Man, Patrick; Newman, Nancy J; Biousse, Valérie; Carelli, Valerio; Moster, Mark L; Vignal-Clermont, Catherine; Klopstock, Thomas; Sadun, Alfredo A; Sergott, Robert C; Hage, Rabih; Degli Esposti, Simona; La Morgia, Chiara; Priglinger, Claudia; Karanja, Rustum; Taiel, Magali; Sahel, José-Alain