Clinical Effects of the Self-administered Subcutaneous Complement Inhibitor Zilucoplan in Patients With Moderate to Severe Generalized Myasthenia Gravis: Results of a Phase 2 Randomized, Double-Blind, Placebo-Controlled, Multicenter Clinical Trial
自我注射皮下补体抑制剂齐鲁普兰治疗中重度全身型重症肌无力患者的临床疗效:一项 II 期随机、双盲、安慰剂对照、多中心临床试验的结果
期刊:Jama Neurology
影响因子:21.3
doi:10.1001/jamaneurol.2019.5125
Howard, James F Jr; Nowak, Richard J; Wolfe, Gil I; Freimer, Miriam L; Vu, Tuan H; Hinton, John L; Benatar, Michael; Duda, Petra W; MacDougall, James E; Farzaneh-Far, Ramin; Kaminski, Henry J; Barohn, Richard; Dimachkie, Mazen; Pasnoor, Mamatha; Farmakidis, Constantine; Liu, Tina; Colgan, Samantha; Benatar, Michael G; Bertorini, Tulio; Pillai, Rekha; Henegar, Robert; Bromberg, Mark; Gibson, Summer; Janecki, Teresa; Freimer, Miriam; Elsheikh, Bakri; Matisak, Paige; Genge, Angela; Guidon, Amanda; David, William; Habib, Ali A; Mathew, Veena; Mozaffar, Tahseen; Hinton, John L; Hewitt, William; Barnett, Deborah; Sullivan, Patricia; Ho, Doreen; Howard, James F Jr; Traub, Rebecca E; Chopra, Manisha; Kaminski, Henry J; Aly, Radwa; Bayat, Elham; Abu-Rub, Mohammad; Khan, Shaida; Lange, Dale; Holzberg, Shara; Khatri, Bhupendra; Lindman, Emily; Olapo, Tayo; Sershon, Lisa M; Lisak, Robert P; Bernitsas, Evanthia; Jia, Kelly; Malik, Rabia; Lewis-Collins, Tiffany D; Nicolle, Michael; Nowak, Richard J; Sharma, Aditi; Roy, Bhaskar; Nye, Joan; Pulley, Michael; Berger, Alan; Shabbir, Yasmeen; Sachdev, Amit; Patterson, Kimberly; Siddiqi, Zaeem; Sivak, Mark; Bratton, Joan; Small, George; Kohli, Anem; Fetter, Mary; Vu, Tuan; Lam, Lucy; Harvey, Brittany; Wolfe, Gil I; Silvestri, Nicholas; Patrick, Kara; Zakalik, Karen; Duda, Petra W; MacDougall, James; Farzaneh-Far, Ramin; Pontius, Angela; Hoarty, Michelle