In situ gene editing of hematopoietic stem cells via AAV-delivered CRISPR guide RNAs
利用腺相关病毒载体递送的CRISPR引导RNA对造血干细胞进行原位基因编辑
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2025016775
Karimzadeh, Alborz; Kim, Rebekah; Garcia, Vivian; Florea, Michael; Peacker, Bryan L; Kobayashi, Shio; Watkins, Drake; Messemer, Kathleen; Zeng, Jing; Bauer, Daniel E; Serwold, Thomas; Wagers, Amy J