Current Status of Clinical Gene Therapy for Hemophilia and Globin Disorders
血友病和珠蛋白疾病临床基因治疗的现状
期刊:Journal of Blood Medicine
影响因子:2.7
doi:10.2147/JBM.S576017
Winkler, Rebecca; Herath, Ishan; Kaczmarek, Radoslaw; Xiao, Weidong; Herzog, Roland W; Severeid, Paige E