日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Divergent mechanisms of neural adaptation and instability in the mammalian retina.

哺乳动物视网膜神经适应和不稳定性机制的差异

Khoussine Jacob, Sawant Abhilash, Gupta Sapan, Zhai Haoshen, Shahi Pawan K, Pattnaik Bikash R, Sinha Raunak, Hoon Mrinalini

Evaluation of subretinally delivered Cas9 ribonucleoproteins in murine and porcine animal models highlights key considerations for therapeutic translation of genetic medicines.

在小鼠和猪动物模型中对视网膜下注射的 Cas9 核糖核蛋白进行评估,突显了基因药物治疗转化中的关键考虑因素

Wei Spencer C, Cantor Aaron J, Walleshauser Jack, Mepani Rina, Melton Kory, Bans Ashil, Khekare Prachi, Gupta Suhani, Wang Jonathan, Soares Craig, Kiwan Radwan, Lee Jieun, McCawley Shannon, Jani Vihasi, Leong Weng In, Shahi Pawan K, Chan Jean, Boivin Pierre, Otoupal Peter, Pattnaik Bikash R, Gamm David M, Saha Krishanu, Gowen Benjamin G, Haak-Frendscho Mary, Janatpour Mary J, Silverman Adam P

Preventing vision loss in a mouse model of Leber Congenital Amaurosis by engineered tRNA

利用基因工程改造的tRNA预防Leber先天性黑蒙小鼠模型的视力丧失

Akyuz, Enes; Shahi, Pawan K; Gissot, Lionel; Saneh, Ahmad Al; Sinha, Divya; Hanstad, Giovanni M; Kabra, Meha; Zepeda, Maria A Fernandez; Gamm, David M; Young, Samuel M; Ahern, Christopher A; Pattnaik, Bikash R

Selectively compromised inner retina function following hypoxic-ischemic encephalopathy in mice: A noninvasive measure of severity of the injury

小鼠缺氧缺血性脑病后选择性内层视网膜功能受损:一种无创性损伤严重程度评估方法

Taparli, Onur E; Shahi, Pawan K; Cagatay, Nur Sena; Aycan, Nur; Ozaydin, Burak; Yapici, Sefer; Liu, Xinying; Cikla, Ulas; Zafer, Dila; Eickhoff, Jens C; Ferrazzano, Peter; Pattnaik, Bikash R; Cengiz, Pelin

Gene Augmentation and Readthrough Rescue Channelopathy in an iPSC-RPE Model of Congenital Blindness

基因增强和通读挽救了iPSC-RPE先天性失明模型中的通道病

Shahi, Pawan K; Hermans, Dalton; Sinha, Divya; Brar, Simran; Moulton, Hannah; Stulo, Sabrina; Borys, Katarzyna D; Capowski, Elizabeth; Pillers, De-Ann M; Gamm, David M; Pattnaik, Bikash R